• Young Boy Becomes First DMD Patient to Receive Investigational Systemic Microdystrophin Gene Therapy
  • Givinostat Phase 3 Trial Recruiting Duchenne Patients in North America, Europe
  • Capricor Adds 7 New Patent Applications from Cedars-Sinai for DMD and Cardiac Disorders
  • Benitec’s BB-301 Granted FDA Orphan Drug Status for Treatment of OPMD
  • Creating a Good Support System
  • Pharma Giants Form UK-Based ‘Project Hercules’ to Generate Evidence for DMD Treatments
  • Duchenne May Affect the Brain Too, Study Contends
  • Analysis of Failed DMD Therapy Kyndrisa Shows Potential Benefit for Younger, Less Impaired Boys
  • Working Muscle Grown from Skin Sample, Raising Hopes for Regenerative Treatments
  • Being Organized for Doctor’s Appointments
  • Acceleron Therapy Increases Facioscapulohumeral Dystrophy Patients’ Muscle Mass, Trial Shows
  • Stoke Receives $40M to Fund New Therapies for MD, Other Genetic Diseases