• Investigational Therapy SR8278 Shown to Regenerate Muscle in DMD Mice Study
  • High Levels of Sarcolipin Protein Underlie Muscle Wasting, Cardiac Disease in DMD
  • Muscle MRI Can Predict Functional Deterioration in Patients with Becker MD, Study Says
  • PPMD Matching Donations Through Dec. 31 for Gene Therapy in Duchenne
  • Staying Warm Even when It’s Rough Outside
  • Long-term Glucocorticoid Therapy in Duchenne Cuts Death Risk by 50% or More, Study Suggests
  • Green Bay Packers’ Clay Matthews Wears Cleats Designed by DMD Boys to Raise Money for CureDuchenne
  • Photography Book, ‘An Ordinary Day,’ Portrays Kids with Rare Genetic Diseases
  • Solid Biosciences Readies Clinical Trial of SGT-001, a Potential Duchenne MD Gene Therapy
  • Capricor Set to Launch Phase 2 Trial of Cell Therapy CAP-1002 in Advanced DMD Patients
  • First Healthy Subject Dosed in Study Evaluating ELX-02 for Treatment of Several Conditions, Including DMD
  • Benitec Seeks Regulatory Approval to Advance Its Gene Therapy Candidate for OPMD