• #NORDSummit – More Than 700 Expected to Attend Oct. 15-16 Rare Disease Summit in Washington
  • Nonprofit Coalition to Cure Calpain 3 Funds 2 Gene Therapy Research Projects for LGMD2A
  • Potential DMD Therapy Vamorolone Shows Positive Effects in Phase 2a Trial, Study Reports
  • A Girl’s Best Friend: Thoughts on Mobility Assistance Dogs
  • Obsessive Compulsive Disorders Evident in Duchenne Patients and in Need of Treatment, Study Says
  • Gene Editing Restored Dystrophin Levels in Dog Model of Duchenne MD, Study Reports
  • STRIVE Awards Recognize Efforts of Duchenne MD Patient Groups Worldwide
  • Listening and Surrendering to My Body Isn’t Always Easy
  • Numotion, Sing Me a Story Partner to Help Children with Neuromuscular Diseases Turn Life Stories to Songs
  • Pfizer Stops Phase 2 Clinical Studies of Domagrozumab in DMD Boys
  • PPMD and Jett Foundation Among Groups Gearing Up for Sept. 7, World Duchenne Awareness Day
  • Finding Doctors Who Understand Your Disease