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  Collaboration Provides Cough Assist Machines to Neuromuscular Disease Patients

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Sarepta’s Gene Therapy for DMD Showing to Safety, Efficacy at One Year

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  MDA Holds Q&A on Navigating COVID-19, and Area Reopenings, Safely

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  COVID-19 and MD
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  Coalition Will Address Racial Disparities in Rare Disease Communities

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Viltolarsen Earns European Orphan Drug Status as Duchenne Treatment

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  DMD Gene Therapy Research to Get $1M From PPMD, Duchenne UK

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Santhera, Rutgers Partner on LAMA2 Muscular Dystrophy Gene Therapy

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Why Self-monitoring Our Functioning Levels Is Important

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Adults​ ​With​ ​Muscular Dystrophy
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  SIDEROS Trial of Puldysa in Duchenne Patients Completes Enrollment

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  DMD Trial Supports ATL1102’s Safety in Improving Muscle Strength

   MD forums Moderator replied 3 years, 10 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Pfizer’s DMD Gene Therapy Shows Promise in Improving Motor Abilities

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Video Games Connect Chronically Ill Children Isolated at Home, Hospital

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  CAP-1002 Improves Muscle, Lung, Heart Function in Young DMD Patients, HOPE-2 Trial Data Show

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Unity and EU-wide Efforts Focus of Online Rare Disease Meet

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Experts’ Advice for Duchenne, Becker Patients Amid COVID-19 Pandemic

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Rare Diseases Research Network Opens Online Survey on COVID-19

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  COVID-19 and MD
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  NORD Webinar Outlines COVID-19 Response on Financial, Policy Fronts

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  CureDuchenne Ventures Gives $1M to Support Non-viral Gene Therapy

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  In DMD, Increlex Improves Growth, but Not Muscle Function, Study Finds

   MD forums Moderator replied 3 years, 11 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  DMD Mice See Improvements From AdipoRon Treatment, Study Shows

   MD forums Moderator replied 3 years, 12 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  In DMD Boys, Vyondys 53 Boosts Dystrophin Production, Early Data Show

   MD forums Moderator replied 3 years, 12 months ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  MDA Let’s Play Uses Gaming to Raise Funds for Neuromuscular Disorders

   MD forums Moderator replied 4 years ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Clinical Trial into Natural History of LGMD2i Enrolling in US, Denmark

  Ralph Yaniz replied 4 years ago 1 Member · 1 Reply

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions
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  Pediatric Rare Disease Therapies on Rise, But Most Repurposed, Study Finds

   MD forums Moderator replied 4 years ago 0 Member · 0 Replies

  Diagnosis​ ​Info​ ​and​ ​General​ ​Questions