• Exondys 51 Superior to Glucocorticoids in Preserving Respiratory Health of Duchenne Boys, Analysis Shows
  • $500K Gift to MDA Summer Camp Will Honor Robert Bennett Legacy
  • The Speak Foundation Speaks Loudly: A Prelude to September in Chicago
  • Macedonian Gaucher Activist Publicizes Plight of Rare Disease Patients
  • Potential DMD Treatment, Pamrevlumab, Helps to Preserve Lung, Heart and Upper Limb Function in Youth, Early Trial Data Show
  • Here’s How I Explain My Experience with Duchenne to Others
  • MDA Awards Locana $550K to Advance Potential RNA-targeting Therapy for Myotonic Dystrophy
  • World’s First Alport Stamp Is Macedonian Mom’s Latest Win for Rare Disease Patients
  • Raising Levels of Protein, Sarcospan, Seen to Benefit Cardiac Muscles in Mouse Model of  DMD
  • You Can Experience the Beauty of the Outdoors, Even with Duchenne
  • Enrollment Progressing Quickly in PolarisDMD Trial Testing Edasalonexent, Catabasis Says
  • Edasalonexent, Potential DMD Therapy in Phase 3 Trial, Seen to Preserve Bone Health in Test in Mice Against Corticosteroid