• What I’ve Learned Since My Son’s LAMA2 MD Diagnosis
  • MDA Engage Offers Free Educational Events
  • #MDA2021 – MDA Virtual Conference to Feature Latest in Clinical Care, Research
  • I’m Ready to Go Forward After My 2nd Dose of the COVID-19 Vaccine
  • Pink, Green, Blue and Purple Lights Illuminated World for Rare Disease Day
  • Vamorolone Trial for DMD Finishes Pivotal First Part, Results Awaited
  • A Hefty Guitar Impacts My Ability to Keep the Music Going
  • Dosing Begins in Phase 2 Trial Testing Oral Therapy BBP-418 for LGMD2i
  • Rare Disease Day ‘Patient Hero’ Raises Awareness Through Fashion
  • Exon Skipping Dominates DMD Treatment, But What’s on Horizon?
  • FDA Approves Amondys 45 for Duchenne Patients With Exon 45 Mutation
  • Givinostat Continues to Delay DMD Progression in Long-term Study, New Data Show