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WVE-210201 Receives FDA Orphan Drug, Rare Pediatric Disease Designations for DMD
NewsWave Life Sciences’ treatment candidate WVE-210201 has been granted both orphan drug designation and rare pediatric disease designation for ... Read more -
Seeing Both Sides of the Plastic Straw Controversy
columns, You, Me and MD - a Column by Leah LeilaniA few years ago, if you had asked me what it means to be eco-friendly, I would have given ... Read more -
Jiffy Lube, MDA Join Forces for 7th Annual MUSCLE UP! Campaign
NewsJiffy Lube is teaming up with the Muscular Dystrophy Association (MDA) in the annual MUSCLE UP! campaign for the seventh year in ... Read more -
2 Nonprofits Join Forces to Help Duchenne Patients Fight Insurance Denials
NewsTwo small patient advocacy groups, Little Hercules Foundation and Team Joseph, are stepping up their joint Duchenne Family Assistance Program ... Read more -
First Patient Enrolled in Phase 2 Trial of MNK-1411, Mallinckrodt’s Investigational Therapy for DMD
NewsThe first patient has been enrolled in a Phase 2 trial evaluating the effectiveness and safety of MNK-1411, ... Read more -
Arizona Woman with Duchenne is a Rarity Among the Rare
NewsDuchenne muscular dystrophy affects an estimated 1 in 3,500 male births. But Elizabeth Heller is an outlier even among ... Read more -
How Lyrica Has Affected My Relationship with Food
columns, You, Me and MD - a Column by Leah LeilaniAll my life, I’ve been very lucky not to be burdened with food and eating problems. For a brief ... Read more -
$700,000 MDA Grant to Help Establish LGMD Clinical Research Network
NewsNicholas Johnson, vice chair of research and associate professor of neurology at Virginia Commonwealth University in Richmond, was awarded ... Read more -
New Online Resource, DuchenneXchange, and Its Offerings Explained in Aug. 7 Webinar
NewsThe nonprofit group CureDuchenne and Connecticut-based rareLife Solutions have launched DuchenneXchange — a dedicated online platform where those interested in Duchenne muscular dystrophy ... Read more -
Family’s Quest for ‘Overlooked’ Duchenne Treatments Leads to Breast Cancer Medicine Tamoxifen
NewsGavin Ward, a spunky 8-year-old Arkansas boy with Duchenne, enjoys building contraptions with his Lego set and watching video ... Read more -
FDA Places Hold on Phase 1/2 Trial of Sarepta’s Gene Therapy for DMD
NewsA Phase 1/2 trial evaluating Sarepta’s microdystrophin gene therapy candidate for Duchenne muscular dystrophy (DMD) was placed on clinical hold by ... Read more -
Consortium.AI to Advance New Treatments for Duchenne Using Artificial Intelligence
NewsInsilico Medicine and A2A Pharmaceuticals, two leading artificial intelligence (AI) biotechs, are collaborating to create a new company called Consortium.AI, ... Read more
