DMD

October 31, 2018October 31, 2018

Cure Duchenne Kicks Off Inaugural ‘Pinkies Up to CureDuchenne’ Fundraising Campaign

News

A campaign hopes to raise awareness of Duchenne muscular dystrophy (DMD) and promote research toward a cure by asking supporters to paint a nail on one of their little fingers ... Read more

October 1, 2018October 1, 2018

MuscleMap Automated Dystrophin Analysis Tool Can Help in DMD Assessment, Study Suggests

News

Flagship Biosciences has developed an automated method to analyze muscle fibers (myofibers) and quantify key disease-related biomarkers, such as dystrophin, for Duchenne muscular dystrophy (DMD). The algorithm, known as ... Read more

September 28, 2018October 26, 2018

Phase 3 Trial of Edasalonexent in Treating DMD Opening Soon, Catabasis Says

News

Catabasis Pharmaceuticals is launching a global Phase 3 trial to evaluate the potential of edasalonexent to treat boys with Duchenne muscular dystrophy (DMD) regardless of mutation type. The soon-to-open PolarisDMD trial is a ... Read more

August 24, 2018August 24, 2018

Canadian Collaboration Gives Funding Boost to Duchenne MD Research

News

AbCellera Biologics Inc. has announced a collaboration with Fabio Rossi, MD, PhD, and Michael Underhill, PhD, of the University of British Columbia, to develop therapeutic antibodies for the treatment ... Read more

May 7, 2018May 7, 2018

Capricor Recruiting Duchenne Patients for Phase 2 Trial of CAP-1002

News

Capricor Therapeutics’ Phase 2 clinical trial to evaluate the safety and effectiveness of CAP-1002 in boys and young men with Duchenne muscular dystrophy (DMD) has started recruiting participants. The HOPE-2 ... Read more

April 20, 2018April 20, 2018

#AAN2018 – Clinical Trials Re-Analysis Shows Emflaza Potential to Preserve Motor Function in Boys with DMD

News

Treatment with Emflaza (deflazacort) is better at preserving motor function in patients with Duchenne muscular dystrophy (DMD) than standard of care corticosteroid treatments, according to a re-analysis of data ... Read more

April 8, 2018April 9, 2018

PPMD Names PerkinElmer to Conduct Genetic Tests for Its Decode Duchenne Program

News

Parent Project Muscular Dystrophy (PPMD) has selected PerkinElmer to provide genetic testing for its Decode Duchenne program, which offers testing and counseling at no cost to eligible Duchenne muscular dystrophy (DMD) patients and ... Read more

February 12, 2018

New CRISPR Strategy Corrects Wider Range of Mutations Responsible for DMD

News

A new approach to CRISPR-Cas9 gene-editing technology, called myoediting, successfully restored dystrophin production and contraction force in heart muscle cells of Duchenne muscular dystrophy (DMD) patients. The new strategy, developed ... Read more

January 29, 2018January 29, 2018

European Agency Again Recommends Against Approval of Raxone as DMD Therapy

News

An advisory committee of the European Medicines Agency (EMA) has issued another negative recommendation after re-examining a request to extend Raxone (idebenone) for use in treating Duchenne muscular dystrophy (DMD). The EMA’s ... Read more

January 24, 2018January 24, 2018

DMD Learning Deficits May Be Linked to Cerebellum Impairment, Study Suggests

News

A dysfunctional cerebellum leads to implicit learning deficits in children with Duchenne muscular dystrophy (DMD), Italian researchers have suggested. Their study, “Implicit learning deficit in children with Duchenne muscular ... Read more

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