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Barbara la saracina replied to the topic Article: A Pivotal Moment for CRISPR in the Gene Editing Journey in the forum Clinical Trials 1 year, 9 months ago
I think they are vwry close to a cure with CRISPIR technology. The gene part is the easier part. Using a vehicle to deliver the gene repair with a non immunogenic nano particle is already being worked on. Keep pr as ying. It is.coming.
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Yasmin and
Barbara la saracina are now friends 1 year, 11 months ago
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Barbara la saracina replied to the topic DMD Gene Therapy in the forum Clinical Trials 1 year, 11 months ago
Are they doing clinical traiks with this gene therapy on young dechenne patients
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Barbara la saracina became a registered member 1 year, 11 months ago
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Hi there Barbara and welcome to the Muscular Dystrophy Forums. My name is Leah and I moderate the forums alongside Dani. We are happy to have you as a part of this community! Here at the MD Forums, we are like a support group, sharing experiences, giving advice and generally discussing life with MD. Don’t hesitate to join in on any of our m…
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Welcome, Barbara! My name is Dani Liptak. I am a forum moderator, along with Leah! I was diagnosed with a type of MD called facioscapulohumeral dystrophy at the age of 12. Please feel free to respond to any of the open discussions that we currently have in progress! Also, let me know if there is a topic that you would like to discuss or any…[Read more]
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