News Enrollment Starts for Phase 2/3 Trial of Oral Therapy for Congenital DM1

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columns, You, Me and MD - a Column by Leah Leilani Joining a Support Group Can Make a Difference

columns, Hawk's-Eye View - a Column by Hawken Miller A Positive Attitude Makes a World of Difference When Coping with Duchenne

News Cure Rare Disease’s Rich Horgan Pioneers Customized Medicine to Treat Brother with DMD

News Duchenne UK Partners with Catabasis to Support Phase 2 Trial of Edasalonexent in DMD

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Society Is Missing the True Definition of Inclusion

News Montana Rancher’s ‘Calves to Cure DMD’ Funds Duchenne Research

columns, You, Me and MD - a Column by Leah Leilani Regaining Control of My Life with The Happy Planner

News Solid Biosciences Cuts Workforce, Restructures to Focus on SGT-001 Development

News Mount Everest Base Camp Trek Raises $60K for Duchenne Research

News PPMD Funds Gene Editing Research to Improve Cardiac Health, Muscle Function in Duchenne

columns, Hawk's-Eye View - a Column by Hawken Miller Why Daily Stretching Is Important for Those with Duchenne Muscular Dystrophy

News Astellas, Audentes Merger May Lead to New Exon-skipping Treatments for MD

News Top 10 Muscular Dystrophy Stories of 2019

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Surviving Winter with Muscular Dystrophy

News Vyondys 53 Available to Duchenne Patients in the U.S.

News New IGNITE DMD Trial Data Promising for SGT-001, Company Working to Lift Clinical Hold

columns, Living, Learning, Thriving - a Column by Ralph Yaniz The Employment Gap for People with Disabilities Is Too Wide

News Potential DMD Treatment, ATL1102, Showing Safety and Muscle Strength Gain in Phase 2 Trial

columns, You, Me and MD - a Column by Leah Leilani Gift Ideas for Your Loved One with MD

News Wave Life Sciences Discontinues Development of Suvodirsen for DMD

columns, Hawk's-Eye View - a Column by Hawken Miller Finding a Job That’s a Good Fit for You and Your Health

News FDA Authorizes Use of Test to Aid Newborn Screening for Duchenne MD

News FDA, in Reversal, Approves Vyondys 53 to Treat Duchenne Patients with Exon 53 Mutations

News GPM-owned Convenience Stores Run Holiday Campaign to Support Muscular Dystrophy Association

columns, You, Me and MD - a Column by Leah Leilani Finding Relief for My Dry, Flaky Winter Skin

News Gene Therapy Takes Center Stage at 2019 NORD Summit

News Buffalo Bills Team with Med Students to Help MDA and Honor Duchenne Volunteer

News HHS Secretary Alex Azar Touts White House Efforts to Cure Rare Diseases

News Mitochondrial Protein’s Loss Linked to Muscle Weakness and Poor Repair in Early Study

columns, Living, Learning, Thriving - a Column by Ralph Yaniz My Adventure in a Wheelchair

News Avidity Secures $100M Funding to Advance Treatments for Myotonic Dystrophy, DMD

columns, Hawk's-Eye View - a Column by Hawken Miller How to Overcome Being Self-conscious About Using a Power Chair

News New DMD Mouse Model Helps Monitor Real-Time Dystrophin Production, Study Reports

News Experts Barry Byrne, Jerry Mendell Lead NORD Webinar on Gene Therapy

News CureDuchenne Develops Biobank to Aid Duchenne Lab Research

News Method Comparing RNA Differences Between Gene Copies May Help Find Cause of Disease, Study Suggests

News Long-term Treatment with Puldysa Reduces Lung Function Decline in DMD Patients, Study Shows

columns, You, Me and MD - a Column by Leah Leilani Improving My Digestion with Enzyme Supplements

News NS Pharma to Provide Update on its Investigational Therapy Viltolarsen in Webinar

columns, Hawk's-Eye View - a Column by Hawken Miller Expressing an Attitude of Thankfulness This Holiday

News PPMD Revamps Duchenne Registry with New App

News Rare Disease Film Festival Highlights Patient and Researcher Unity

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Let’s Stay on the Cutting Edge of Research

News FDA Puts 2nd Clinical Hold on IGNITE DMD Trial of Gene Therapy SGT-001 Due to Patient Reaction

News Clinical Trial Program Testing RG6206 in DMD Boys Has Been Discontinued

columns, You, Me and MD - a Column by Leah Leilani Attack of the Bloodthirsty Mosquitoes

News Local November 9th MDA Disease Education Events Span East, West Coast

News Experimental Cell Therapy Improves Cardiac Function in Mouse Model of DMD, Study Says

News Investigational Therapy Losmapimod Targets Root Cause of FSHD, Early Study Suggests

columns, Hawk's-Eye View - a Column by Hawken Miller Goals Can Simplify Our Complicated Lives

News BIIB100 Improves Motor Function, Slows DMD Progression in Animal Models, Study Finds

News PPMD Grants Funding for Research on Cardiac Health in People with Duchenne

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Prioritizing Goals in Life with MD

News Translarna Preserves Lung Function, Muscle Strength in DMD Boys, Real-World Data Show

columns, You, Me and MD - a Column by Leah Leilani I Won’t Give Up My Positive Attitude for Others

News Vamorolone Designated Promising Innovative Medicine in UK for DMD Treatment

News Novel Gene Therapy Safely Prevents Muscle Deterioration in Animal Models of DMD, Study Reports

News Vamorolone Extension Trial Supports Muscle Gains in DMD with Fewer Side Effects, Topline Data Show

columns, You, Me and MD - a Column by Leah Leilani Adjusting to Life Without My Gallbladder

columns, Hawk's-Eye View - a Column by Hawken Miller Friendships Matter: You Don’t Have to Deal with Duchenne Alone

News CureDuchenne Developing a Biobank for DMD Research

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Peeling Back the Layers of Societal Barriers for People with Disabilities

News Positive Early Results Support Continuation of Phase 2 Trial of ATL1102 for DMD

News PPMD Grants to Promote Gene Therapy for Heart Disease and Patient Outcomes Research

News Catabasis Joins Jain Foundation to Advance Edasalonexent Development for Dysferlinopathy

News Dyne Therapeutics Supporting FSHD Natural History Study Underway in US, Europe

News Gene Therapy SRP-9003 Showing ‘Very Encouraging’ Results at 9 Months in Limb Girdle MD, Sarepta Reports

columns, Hawk's-Eye View - a Column by Hawken Miller The Right Job Can Help You Find Fulfillment and Purpose

News Request to Approve Viltolarsen, Exon 53 Skipping Treatment for Duchenne MD, Before FDA

News First Baby Tested for Duchenne in PPMD’s Newborn Screening Pilot Program in NY

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Opportunities Abound for Travel and Accessibility

News FDA Awards $1M to Phase 2 Study of Ifetroban in Treating Heart Disease Linked to Duchenne MD

columns, You, Me and MD - a Column by Leah Leilani Honoring Serena Lawrence: How Her Life Changed Mine

News CureDuchenne Plans Oct. 11-13 ‘Futures’ Meet at California’s Disneyland

News PPMD Announces First Adult Certified Duchenne Care Center

News NORD 2019 Rare Disease Summit Set for Oct. 21-22 in Washington, DC

News Final Tests Planned into Potential Gene Therapy for OPMD, Could Support Trial in Patients

columns, Hawk's-Eye View - a Column by Hawken Miller Redefining the Word ‘Independence’

News CureDuchenne Offers One-Stop Informative Guide on Durable Medical Equipment

News Suvodirsen Receives FDA’s Fast Track Status to Treat DMD

columns, Living, Learning, Thriving - a Column by Ralph Yaniz ‘30 Days of MD’ Brings Awareness That Lasts All Year

News Acceleron Stops Clinical Development of ACE-083 as Treatment for FSHD

News New Blood Biomarkers of DMD and Glucocorticoid Response Identified

News Microdystrophin Gene Therapy Improves with nNOS Domain, Review Study Says

columns, Living, Learning, Thriving - a Column by Ralph Yaniz National LGMD Conference Builds the MD Community

News MDA Awards $6.6M to 25 Scientists Working in DMD, Other Neuromuscular Diseases

columns, You, Me and MD - a Column by Leah Leilani My Asthma Flare Inspired Me to Buy a Vogmask

columns, Hawk's-Eye View - a Column by Hawken Miller Regular Checkups Can Help You Stay Well for as Long as Possible

News BBP-418 in Development to Treat LGMD Type 2I, with Natural History Study to Start Soon

News September is MDA National Muscular Dystrophy Awareness Month

News BioNews’ MD Forum Offers Support, Community – and a Place to Vent

News Vamorolone Improves Muscle Function in DMD Boys, Phase 2a Trial Data Show

columns, You, Me and MD - a Column by Leah Leilani My Boyfriend Is Full of Ideas to Help Fight Inaccessibility

News ‘Disorder’ Film Festival Offers Look at Siblings Touched by Rare Diseases

News Jett Foundation’s Mission: ‘Making People Care About Duchenne’

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Inaccessible Accessibility: It’s Time to Get Serious

News At NY Genome Center, Legal Expert Presents Ethical Dilemmas in Gene Editing

News Adults Living with DMD, Parents and Patients, Voice ‘Cautious Optimism’ for Gene Therapy in Interviews