Four years ago, my family enjoyed a week’s vacation at Bethany Beach, Delaware. There were many great moments that made this trip with my children and grandchildren memorable. There were also a couple of misadventures. We spent a day on Virginia’s Chincoteague Island, which is famous for its population of…
Discussion
The gene therapy Elevidys (delandistrogene moxeparvovec-rokl), approved in the U.S. to treat people ages 4 and older with Duchenne muscular dystrophy (DMD), can be safely administered to boys with DMD as young as 2 years old, new data show. A new analysis, which covered nine boys with DMD…
Discussion
It seems to be a theme in our lives: Lifts and elevators work great — until they don’t. I am a mom to many: Lexi, 25; Max, 20; Chance, 19; Rowen, 17; Charlie, 15; Mary, 12; and Callie, 4. Three of my sons, Max, Rowen, and Charlie, have Duchenne…
Discussion
Boys and young men with Duchenne muscular dystrophy (DMD) who switched from a placebo to the experimental cell therapy deramiocel as part of a clinical trial showed smaller declines in measures of upper limb function after making the change, new data show. Data from the study, which included…
Discussion
Last week, I lost my dear friend Aloysius Teo, who passed away at the age of 40. Aloysius didn’t have Duchenne muscular dystrophy, the progressive genetic condition I was born with, which weakens muscles over time, including those used for breathing and heart function. I use a wheelchair…
Becoming educated and informed about muscular dystrophy is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your muscular dystrophy journey.
There is no cure for muscular dystrophy yet, but here you can find more information about current therapeutic approaches, as well as experimental treatments that are in the pipeline.
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