Here’s How I Decorated My Wheelchair This Christmas
In my family, almost every holiday deserves decorations. Even Valentine’s Day is celebrated, with heart stickers on our bathroom mirrors and red-heart garland strewn ... Read more
Updates
-
-
Potential DMD Therapy WVE-210201 Shows Positive Phase 1 Safety Results
WVE-210201, an exon 51 skipping therapy, has shown positive safety and tolerability results in a Phase 1 clinical trial in boys with Duchenne muscular dystrophy (DMD), Wave Life ... Read more -
Budding Journalist Hawken Miller Offers Advice on Living With Duchenne
At 21, Hawken Miller certainly doesn’t look like a typical Duchenne muscular dystrophy patient. For one thing, unlike most boys and young men with ... Read more -
Coping with Duchenne: Parents Swap Stories at ‘Futures’ Conference
Until her son, Will, was diagnosed with Duchenne muscular dystrophy as a 7-year-old, speech pathologist Tiffany Cook had never heard of the disease. Today, ... Read more -
Seasonal Cooking with Mito
The Christmas season has drifted in, and with it come mouth-watering kitchen smells. It’s time to mix the cookie dough, roll out the pie ... Read more
-
UVA Children’s Hospital Recognized for Expert Duchenne Care by Parent Project MD
The University of Virginia (UVA) Children’s Hospital has been named a Certified Duchenne Care Center by Parent Project Muscular ... -
Muscular Dystrophy UK Partners to Make Toilets on England’s Roadways More Accessible to All
Hoping to make travel less difficult throughout England for disabled motorists, including those with muscular ... -
Neurologist Brenda Wong Heads New Specialized Duchenne Clinic at UMass
For nearly half a year, Brenda Wong, MD, has led New England’s first and ... -
Small Ways to Get in the Holiday Spirit
The holidays can be a tumultuous time. Advertisements would have us believe that the ... -
Taiho’s TAS-205 May Represent New Therapy Option for DMD, Phase 1 Data Shows
Early safety and efficacy data from a Phase 1 trial suggest that Taiho Pharmaceutical’s ... -
West Virginia Mom of Duchenne Boy Struggles to Make Ends Meet
Like many mothers of boys with muscular dystrophy, Deborah Hall hasn’t had an easy ...
Subscribe to our mailing list
Get regular updates delivered to your email box.
Thanks! Please check your email for a confirmation email.
FDA Grants Rare Pediatric Disease Status to Myonexus’ MYO-101 for LGMD 2E
News
The U.S. Food and Drug Administration recently granted rare pediatric disease designation to Myonexus Therapeutics’ experimental gene therapy MYO-101 for the treatment of limb girdle muscular dystrophy (LGMD) type 2E, or LGMD2E. The announcement was made by Myonexus and Nationwide Children’s ... Read more