The U.S. Food and Drug Administration (FDA) has given the go-ahead for a mid-stage clinical trial testing the oral therapy forazapadin — designed to protect muscles and potentially enhance their regeneration — in adults with facioscapulohumeral muscular dystrophy (FSHD), marked by muscle weakness that particularly affects the face,…
Discussion
Managing my condition is a full-time job. Muscular dystrophy (MD) has woven its way into more than just my muscles. It takes a mental toll as time goes by. The hours tick away. The cells tick away. I was 12 when I learned of my diagnosis. I…
Discussion
For many people living with rare neuromuscular diseases, the most meaningful part of a recent Chicago gathering was not just the medical updates — it was finding a community that understood their daily struggles. The realization that they were not alone set the tone for MDA Engage: Chicago, a…
Discussion
It’s been a big week for the Vertin Party of 9. We moved into our new home, and after only a week, the blessings seem boundless. I’m so thankful to share this because, as you can imagine, moving a large family is a tremendous undertaking. My husband, Jason, and I have…
Discussion
New treatments for muscular dystrophy (MD) are moving forward, but no single therapy will work for every MD type, and some promising therapies have fallen short in trials, two neuromuscular specialists told patients and families. “Muscular dystrophies are not just one condition,” said Ryan Jacobson, MD, a neuromuscular…
Becoming educated and informed about muscular dystrophy is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your muscular dystrophy journey.
There is no cure for muscular dystrophy yet, but here you can find more information about current therapeutic approaches, as well as experimental treatments that are in the pipeline.
Get regular updates to your inbox.
