News CureDuchenne Ventures Invests in Dyne and Its DMD Therapy Program

columns, You, Me and MD - a Column by Leah Leilani Realizing My Introversion During Self-isolation

News MDA Partners with Invitae to Offer Free Gene Testing, Counseling for MD

columns, Hawk's-Eye View - a Column by Hawken Miller Self-quarantine Has Leveled the Social Playing Field

News, syndicated NORD’s Advice on COVID-19: You’re Stronger Than You Think

News MDA Hosting Online Q&A on COVID-19 Today

News Trial Use of Edasalonexent Not Likely to Raise COVID-19 Risk, Catabasis Reports

columns, Living, Learning, Thriving - a Column by Ralph Yaniz The Muscular Dystrophy Community Counts on Accessibility Improvements

News Phase 1 Results Support Losmapimod as FSHD Treatment

News NORD Partners with ‘Sing Me a Story’ for July 18–20 Living Rare Forum

News Sarepta Working to Ensure Treatment Access, Clinical Trials Continuity Amid COVID-19 Pandemic

News Emflaza Supply Not Affected by COVID-19 Pandemic, PTC Therapeutics Says

News Global Rare Disease Group’s Focus: 1,000 New Therapies by 2027, Despite COVID-19

News Viltolarsen Available to U.S. DMD Patients Under Expanded Access Program

News Machine Learning Helps Diagnose Specific MD Forms, Study Finds

News Capricor Therapeutics Expands Exosome Technology for DMD

columns, You, Me and MD - a Column by Leah Leilani Redefining Success While Living with a Chronic Illness

News AdipoRon Eases Inflammation, Improves Motor Function in DMD Mice, Study Shows

columns, Hawk's-Eye View - a Column by Hawken Miller Celebrating My First Year of Writing Columns

News Vyondys 53 Boosts Dystrophin Production in Boys With DMD, Early Results Show

News MDA Let’s Play Uses Gaming to Raise Funds for Neuromuscular Disorders

columns, Living, Learning, Thriving - a Column by Ralph Yaniz One Year Later: Catch Me if You Can

News Increlex Improves Growth, But Not Muscle Function in DMD, Early Trial Shows

News ‘Napa in Newport’ Raises More Than $1M for CureDuchenne

Muscular Dystrophy News, News Pediatric Rare Disease Therapies Increase, But Most Repurposed, Study Finds

columns, You, Me and MD - a Column by Leah Leilani My Favorite Moments at This Year’s LA Abilities Expo

News Clinical Trial into Natural History of LGMD2i Enrolling in US, Denmark

News PerkinElmer Launches New Genetic Test for FSHD Type 1

News L-arginine in Diet May Improve DMD Gut Function, Mouse Study Suggests

News Addressing Metabolic Changes Could Be Effective Treatment in DMD, BMD, Study Suggests

News Video: BioNews’ Social Media Campaign Highlights #WhatMakesMeRare

News FSHD Advocate to Speak at FDA Drug Development Meeting in April

News Elsevier Opens Books, Review Articles to Rare Disease Researchers Starting Feb. 29

News Small Molecule Raises Utrophin Levels to Rescue Muscle Function in DMD, Mouse Study Suggests

columns, Hawk's-Eye View - a Column by Hawken Miller Life Isn’t Fair, but I Can Make the Best of It

News CITGO Marketer Graham Enterprise Raised $123K Last Year for MDA

News Advice on Starting Nonprofit Groups for Rare and Other Diseases Focus of NORD Webinar

News Phase 2b Trial of Fulcrum’s Oral FSHD Treatment, Losmapimod, Fully Enrolled

columns, Living, Learning, Thriving - a Column by Ralph Yaniz On Rare Disease Day, Let’s Dare to Be Rare

News New CRISPR-Cas9 Delivery Method Improves Muscle Function in DMD Mice, Study Reports

News Simultaneous Analysis of Multiple Clinical Trial Endpoints Is Feasible, Study Finds

columns, You, Me and MD - a Column by Leah Leilani I Advocate for Disability Rights with Apparel and Accessories

News Adenylosuccinic Acid Therapy Improves Symptoms of Duchenne Muscular Dystrophy in Mice, Study Finds

News Nonprofits Give $200K to DMD Gene Therapy Project

News Antimalarial Medicine Chloroquine Improves Muscle Strength in Animal Models of DM1, Study Finds

News PTC Therapeutics’ Global Program Strives to Fund Innovative Projects of Patient Advocacy Organizations

News Patients, Supporters Worldwide Recognizing Rare Disease Day 2020

News MDA Launches 38th Annual #Shamrocks Fundraising Campaign, Aims to Raise $8M

News Duchenne ‘Consumer Advocates’ Have Say in Federal Research Funding for DMD

columns, Hawk's-Eye View - a Column by Hawken Miller As Adults with DMD, We Have a Responsibility to Mentor Younger Generations

News Registration for PPMD Advocacy Conference Now Open

News TAS‐205 Safe, May Slow Muscle Loss in DMD Patients, Phase 2 Data Suggest

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Addressing the Funding Crisis for Social Security

News CureDuchenne Teams Up with Vivli to Share DMD Clinical Trial Data

News FDA Accepts New Drug Application for Potential DMD Treatment Viltolarsen

News FDA Efforts to Bring Patients into Treatment Decisions Focus of NORD Webinar

News BIND Project Focuses on Brain Effects of Muscular Dystrophies

News World Duchenne Organization Takes Lead in European Efforts to Better Treat DMD

News Orsini Specialty Pharmacy Now Provides Vyondys 53 to Treat Duchenne

News With Post-Brexit Move to Amsterdam Complete, EMA Renews Rare Disease Focus

News From Care Centers to Research Awards and Summer Camp, MDA Leads by Helping Others

News Combo Treatments, Gene Therapies and What’s Ahead for Muscular Dystrophy: Talk with MDA

News Blocking IGF2R Protein Could Be Therapeutic Strategy, Improve Muscle Strength in DMD, Mouse Study Suggests

columns, You, Me and MD - a Column by Leah Leilani Difficulties Strengthen Interabled Relationships

News Gene Editing Restores Dystrophin in Pig Model of Duchenne and Patient Cells, Study Reports

columns, Hawk's-Eye View - a Column by Hawken Miller Developing My Talents Has Helped Me to Thrive

News CITGO Marketer CN Brown Raises More Than $300K for MDA in 2019

News FDA Grants Orphan Drug Status to Losmapimod as Potential FSHD Therapy

News Nonprofits RARE Courage, All Wheels Up Partner on Survey Seeking to Improve Air Travel for Wheelchair Users

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Now Is the Best Time to Set 2020 Goals

News Cx43 Protein May Be Key to Preventing Heart Disease in DMD, Mouse Study Suggests

News Saphyr System to Aid GeneDx in Detecting Mutations Causing Various Muscular Dystrophies

News New York Pilot Program Uses PerkinElmer’s Recently Approved DMD Screening Test for Newborns

News Genethon and Sarepta Extend Collaboration to Develop DMD Gene Therapy

News Enrollment Starts for Phase 2/3 Trial of Oral Therapy for Congenital DM1

columns, You, Me and MD - a Column by Leah Leilani Joining a Support Group Can Make a Difference

columns, Hawk's-Eye View - a Column by Hawken Miller A Positive Attitude Makes a World of Difference When Coping with Duchenne

News Cure Rare Disease’s Rich Horgan Pioneers Customized Medicine to Treat Brother with DMD

News Duchenne UK Partners with Catabasis to Support Phase 2 Trial of Edasalonexent in DMD

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Society Is Missing the True Definition of Inclusion

News Montana Rancher’s ‘Calves to Cure DMD’ Funds Duchenne Research

columns, You, Me and MD - a Column by Leah Leilani Regaining Control of My Life with The Happy Planner

News Solid Biosciences Cuts Workforce, Restructures to Focus on SGT-001 Development

News Mount Everest Base Camp Trek Raises $60K for Duchenne Research

News PPMD Funds Gene Editing Research to Improve Cardiac Health, Muscle Function in Duchenne

columns, Hawk's-Eye View - a Column by Hawken Miller Why Daily Stretching Is Important for Those with Duchenne Muscular Dystrophy

News Astellas, Audentes Merger May Lead to New Exon-skipping Treatments for MD

News Top 10 Muscular Dystrophy Stories of 2019

columns, Living, Learning, Thriving - a Column by Ralph Yaniz Surviving Winter with Muscular Dystrophy

News Vyondys 53 Available to Duchenne Patients in the U.S.

News New IGNITE DMD Trial Data Promising for SGT-001, Company Working to Lift Clinical Hold

columns, Living, Learning, Thriving - a Column by Ralph Yaniz The Employment Gap for People with Disabilities Is Too Wide

News Potential DMD Treatment, ATL1102, Showing Safety and Muscle Strength Gain in Phase 2 Trial

columns, You, Me and MD - a Column by Leah Leilani Gift Ideas for Your Loved One with MD

News Wave Life Sciences Discontinues Development of Suvodirsen for DMD

columns, Hawk's-Eye View - a Column by Hawken Miller Finding a Job That’s a Good Fit for You and Your Health

News FDA Authorizes Use of Test to Aid Newborn Screening for Duchenne MD

News FDA, in Reversal, Approves Vyondys 53 to Treat Duchenne Patients with Exon 53 Mutations

News GPM-owned Convenience Stores Run Holiday Campaign to Support Muscular Dystrophy Association

columns, You, Me and MD - a Column by Leah Leilani Finding Relief for My Dry, Flaky Winter Skin