• Audentes Presents RECENSUS Study of Boys With X-Linked Myotubular Myopathy
  • FDA OK Prompts Akashi to Resume Developing HT-100 for Duchenne MD
  • Massachusetts Mom, Daughter Open Up About FSHD and How It Affects Their Lives
  • PPMD’s ‘Run For Our Sons’ Fundraising Events Can Use Your Help
  • $119K Grant Awarded to Gene Therapy Project for Charcot-Marie-Tooth Disease
  • PTC Therapeutics to Acquire Emflaza for the Treatment of Duchenne MD in the US
  • Napa Valley Fundraiser Yields $1M for Duchenne Research
  • Duchenne Children’s Balance Deteriorates as Disease Progresses, Study Finds
  • Catabasis to Present MoveDMD Trial Data of Edasalonexent for Duchenne at Conference
  • MDA Awards $7M in Grants for 29 Disease-Targeting Research Projects
  • Duchenne’s Impact on Heart Reviewed, Suggesting Treatment Options
  • Bone Health Varies Greatly Among FSHD Patients, Study Suggests