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  Gene Therapy SRP-9003 Showing ‘Very Encouraging’ Results at 9 Months in Limb Girdle MD, Sarepta Reports

  Posted by MD forums Moderator on October 14, 2019 at 12:10 pm

  

  A 9-month update on three LGMD type 2E childen given one low-dose of the gene therapy SRP-9003 in a clinical trial shows “significant” gains in NSAD scores. Read more here.

  What do you think of this study and its findings?

  MD forums Moderator replied 4 years, 6 months ago 1 Member · 0 Replies
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