A new mouse model of Duchenne muscular dystrophy (DMD) can…
Articles by Alice Melão
Treatment with Translarna (ataluren) preserves lung function and muscle strength in boys with Duchenne muscular dystrophy (DMD),…
Experimental therapy ATL1102 improved upper limb strength and function in six boys with Duchenne muscular dystrophy (DMD) unable…
Cumberland Pharmaceuticals announced that it has been awarded a $1 million grant by the U.S. Food and Drug Administration…
The ongoing Phase 2 HOPE-2 study has been cleared to continue exploring the potential of CAP-1002 therapy in boys…
A signaling pathway determines whether muscle stem cells differentiate and mature into working muscle cells, an early study in mice…
Engineered small versions of dystrophin protein, known as microdystrophins, have shown the ability to enhance muscle strength and function in…
Severe Duchenne muscular dystrophy (DMD) is linked to increased susceptibility to a rare and aggressive type of muscle cancer…
Early safety and efficacy data from a Phase 1 trial suggest that Taiho Pharmaceutical’s investigational compound TAS-205 may hold…
Researchers at The University of Western Australia (UWA) have been awarded close to $490,000 from two organizations to explore the potential…