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August 19, 2025 by Catalyst Pharmaceuticals, Inc.

Meet Gaven, an Actual AGAMREE® (vamorolone) Patient

Insights Into Living With Duchenne Muscular Dystrophy (DMD) Gaven lives in Texas, sharing a home with his mother, father, and 12-year-old brother, Tristan. Like many 10-year-old boys, he enjoys visits to the museum, going to restaurants, and most of all, riding motorcycles. His parents describe him as logical…

June 1, 2025 by Catalyst Pharmaceuticals, Inc.

Catalyst Pathways®: Your Path to a Better Tomorrow

Duchenne muscular dystrophy (DMD) is a rare genetic disorder that causes progressive muscle weakness. People living with DMD and their families face a variety of challenges every day. A path to prompt, affordable treatment should not be one of them. That is why Catalyst Pharmaceuticals created Catalyst Pathways®,…

Recent Posts

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  • My family caregivers are feeling the pressure
  • BBP-418 improves walking ability in LGMD2i patients in Phase 3 trial
  • I’m giving everything I have for Duchenne MD — in my own way


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