A potential next-generation therapy, golodirsen (SRP-4053) facilitates and increases dystrophin production in Duchenne muscular dystrophy (DMD) patients, an interim analysis…
Articles by Catarina Silva, MSc
A stem cell therapy improved the heart function, walking capacity and survival of mice with Duchenne muscular dystrophy, a study…
Researchers found that giving Duchenne muscular dystrophy (DMD) patients glucocorticoid therapy keeps them mobile for a longer period of time…
•The Muscular Dystrophy Association has awarded 13 grants totaling $3.5 million to researchers working on treatments for neuromuscular diseases such…
Research into molecules that appear to target the gene known to cause facioscapulohumeral dystrophy (FSHD) may lead to a treatment…