Sarepta Therapeutics of Cambridge, Massachusetts, reports it has been notified by the Food and Drug Administration (FDA) that the…
Articles by Charles Moore
An expert panel convened by the U.S. Food and Drug Administration (FDA) recently voted against granting accelerated approval to the…
UPDATE: Since this story was filed, Reuters news service is reporting that even more quickly than we…
Ten-year-old Gabe Griffin of Alabama visited Washington, D.C., with his parents last month hoping to encourage Congress…
Charles Thornton, M.D., the Saunders Family Distinguished Professor in Neuromuscular Research at the University of Rochester…
Tens of thousands of businesses across the U.S. are participating in this year’s 34th annual Muscular…
Capricor Therapeutics, Inc., a clinical-stage biotechnology company, has treated the first Duchenne muscular dystrophy patient with related cardiomyopathy with its…
PTC Therapeutics, Inc. announced Wednesday that it has received a Refuse to File letter from the U.S. Food and Drug…
One hundred and nine members of the U.S. House of Representatives signed a letter to the U.S. Food and Drug Administration…
In recognition that people with muscular dystrophy are living longer than even recently thought possible, the Muscular Dystrophy Association (MDA) has…