Recent Posts
- DMD gene therapy GNT0004 set to enter Phase 3 trial in Europe, US
- Taking control when living with limb-girdle muscular dystrophy
- Changes this year helped me learn my limitations as a caregiver
- Regenxbio starts pivotal trial testing DMD gene therapy RGX-202
- How I experienced inclusion (and didn’t) during my education
- New technology may inform effective MD gene therapies: Study
- Being mindful of kidney stones while living with DMD
- FDA OKs trial to test gene therapy candidate in LGMD children
- Sarepta stops development of exon 51-skipping therapy for DMD
- Coping with grief and the day-to-day life of LGMD