Recent Posts
- RNA-based approach shows promise for DM1 in cell models
- An emergency preparedness plan is crucial for those with disabilities
- Gene therapy at low dose helps two OPMD patients with swallowing
- Every week, we try to organize chaos in our family of 9
- Capricor now seeking FDA approval of DMD therapy deramiocel
- C-Path to lead new task force seeking to advance LGMD therapies
- Educating all ages about living with muscular dystrophy
- This time, new medical equipment is hard for me to accept
- Rare pediatric disease designation granted to LAMA2-CMD therapy
- DMD treatment WVE-N531 boosts dystrophin: Interim trial data