Posts by: Ines Martins, PhD

Ines Martins, PhD

Inês Martins holds a BSc in Cell and Molecular Biology from Universidade Nova de Lisboa and is currently finishing her PhD in Biomedical Sciences at Universidade de Lisboa. Her work has been focused on blood vessels and their role in both hematopoiesis and cancer development.

May 21, 2020May 21, 2020

SIDEROS Phase 3 Trial of Puldysa in Duchenne Patients Completes Enrollment

News

The SIDEROS Phase 3 clinical trial, investigating if oral Puldysa (idebenone) can be added to a stable glucocorticoid regimen to more effectively slow lung function decline in boys and men with Duchenne ... Read more

May 12, 2020May 12, 2020

IGNITE DMD Trial Remains on Hold, FDA Requests More Gene Therapy Data

News

The U.S. Food and Drug Administration (FDA) is requesting more information on the process used to manufacture the gene therapy SGT-001, as it reviews the clinical hold placed on the Phase ... Read more

May 7, 2020May 7, 2020

Experts Offer Advice for Duchenne, Becker Patients Amid COVID-19 Pandemic

News

People with Duchenne and Becker muscular dystrophy should not forego their routine health assessments during the COVID-19 pandemic, but are encouraged to transition their care to telemedicine and to medical tests performed at ... Read more

May 5, 2020May 5, 2020

CureDuchenne Ventures Gives $1M to Support Non-viral Gene Therapy Work

News

CureDuchenne Ventures has given $1 million in seed funding to support the development of Myosana Therapeutics‘ potential non-viral gene therapy for people with Duchenne muscular dystrophy (DMD). The money is expected to ... Read more

August 10, 2016August 10, 2016

Pfizer Acquires Bamboo Therapeutics, Readies Clinical Trial of Gene Therapy for DMD

News

Bamboo Therapeutics has been fully acquired by Pfizer, considerably expanding that company’s holdings in gene therapy. With the acquisition, Pfizer gains several potential therapeutic agents for rare diseases, including one for Duchenne muscular dystrophy (DMD), ... Read more

June 9, 2016June 9, 2016

Protein linked to Impaired Muscle Regeneration in Duchenne Muscular Dystrophy

News

A new study from the University of Liverpool, has identified high amounts of a neutrophil-derived protein in the muscle of a Duchenne muscular dystrophy (DMD) mouse model. The finding ... Read more

June 1, 2016June 1, 2016

First Duchenne MD Patient to Be Approved for Adult Stem Cell Treatments in US Turns 30

News

Ryan Benton, the first patient to be approved in the United States for allogenic adult stem cell transplantation as a Duchenne muscular dystrophy (DMD) treatment, turned 30 this year — ... Read more

May 26, 2016May 26, 2016

Scientists See Improved Muscular Regeneration, Increased Life Span in Mice After Targeting Mitochondria Function

News

Nicotinamide riboside (NR), a compound that has been shown effective in boosting metabolism, can also induce muscular regeneration and enhance life span in mice, according to the study “NAD+ ... Read more

May 25, 2016May 25, 2016

Researchers Develop First Human Stem Cell-Derived Model of a Muscular Dystrophy

News

Genea Biocells has developed a human stem cell-based cellular model for a type of muscular dystrophy, known as facioscapulohumeral muscular dystrophy (FSHD), that may be a suitable tool for ... Read more

May 11, 2016May 11, 2016

Defective RNA Processing Linked to Cardiac Problems Seen in Myotonic Dystrophy Patients

News

Researchers have discovered the molecular mechanisms responsible for the heart dysfunctions that mark myotonic dystrophy, and reported they appear to be linked to a defective processing of the cardiac sodium channel (SCN5A) ... Read more

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