The supply of Emflaza (deflazacort), a treatment for people with Duchenne muscular dystrophy (DMD), will not be…
Articles by Iqra Mumal, MSc
Parent Project Muscular Dystrophy (PPMD) has awarded a total of $148,000 to researchers at Nationwide Children’s Hospital and…
Extracellular RNAs found in urine may be able to serve as non-invasive biomarkers of how patients with muscular dystrophy —…
Taking care of patients with Duchenne muscular dystrophy (DMD) can have significant effects on caregivers, leading to a lower…
Wave Life Sciences’ treatment candidate WVE-210201 has been granted both orphan drug designation and rare pediatric disease designation for…
Cognitive behavioral therapy improved physical activity and social participation in patients with myotonic dystrophy type 1, indicating its potential…
American researchers have developed a new way of delivering a gene editing therapy that significantly increases the time a repaired…
A new way of transferring the dystrophin gene — the largest known human gene — into muscle stem cells may…
Aberrant signaling in the IL-6 pathway, which is involved in muscle cell maturation, contributes to the severe symptoms seen in congenital…
Scientists at Saint Louis University believe that an investigational therapy called SR8278 holds potential for treating Duchenne muscular dystrophy (DMD) after…