Researchers have found that skeletal muscle magnetic resonance imaging (MRI) correlates with motor function and can help predict the degree…
Articles by Iqra Mumal, MSc
In recent years scientists have learned that the protein utrophin can substitute for the dystrophin protein that is missing in muscular…
Wave Life Sciences has started a Phase 1 clinical trial of a treatment for a gene malfunction linked to the…
Sarepta Therapeutics is working with Duke University’s biomedical engineering program program on gene editing therapies for Duchenne muscular dystrophy. The editing approach…
Researchers have found that reducing levels of elevated sarcolipin protein may be a potentially effective therapeutic strategy in the treatment…
Tricyclo-DNA (tcDNA), a class of therapeutics known as antisense oligonucleotides (AONs), has shown an important degree of effectiveness and a promising…
A new version of the CRISPR-Cas9 gene-editing technology called CRISPR-Gold has successfully restored the correct sequence of the dystrophin gene…
The drug discovery and development biopharma Summit Therapeutics is giving several presentations related to the ongoing…
In what could be the first step on the long road to finding a potential cure, researchers have found that…
Researchers have found Duchenne muscular dystrophy (DMD) patients with heart disease have very high levels of ST2, an interleukin 1 receptor-like…