Joe Pierce,  —

Recent Posts

• FDA awards LAMA2-CMD therapy MDL-101 orphan drug status
• Duchenne affects my entire life, down to a DIY project
• DM1 progression varies with sex, age at disease onset: Study
• A new beginning of shared purpose at Shalom Medcare
• EMA agency continues to oppose renewing Translarna’s approval
• Changing society and its views on disability, one column at a time
• I wish all of my sons could have played football
• RNA-based approach shows promise for DM1 in cell models
• An emergency preparedness plan is crucial for those with disabilities
• Gene therapy at low dose helps two OPMD patients with swallowing