Rare Disease Day 2023
Recent Posts
- MDA 2023: Translarna may help preserve motor function in DMD
- MDA 2023: DMD boys show motor gains with cell therapy DT-DEC01
- To be a better caregiver, I need to prioritize my health, too
- MDA 2023: SRP-9001 shows long-term gains in DMD patients
- As an MD survivor, I can relate to Singaporean assistance dog users
- MDA 2023: Exondys 51 may boost survival for DMD patients
- Living in a rural area can be challenging for those with DMD
- Researchers to launch new cohort in DMD natural history study
- The advantages of keeping an open mind when meeting a new doctor
- 2 MDA research grants will tackle DMD gene therapy safety issues