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November 15, 2018November 15, 2018

CureDuchenne and Avidity Biosciences Hosting Webinar Friday on Potential DMD Therapies

News

CureDuchenne and Avidity Biosciences will host a webinar Friday to brief the Duchenne muscular dystrophy (DMD) community on Avidity’s preclinical development of DMD therapy candidates. The webinar will take ... Read more

November 14, 2018November 14, 2018

Extracellular RNAs in Urine May Work as Biomarker for Duchenne and Myotonic Dystrophy Patients

News

Extracellular RNAs found in urine may be able to serve as non-invasive biomarkers of how patients with muscular dystrophy — especially those with an adult-onset and the more common ... Read more

November 12, 2018November 12, 2018

Phase 3 Trial of Edasalonexent in Boys with DMD and Any Mutation Enrolling in US, Catabasis Reports

News

A pivotal Phase 3 trial of edasalonexent, a potential oral disease-modifying treatment for Duchenne muscular dystrophy (DMD) regardless of mutation type, is enrolling boys ages 4 to 7 in the ... Read more

November 9, 2018November 9, 2018

Jiffy Lube’s ‘Muscle Up!’ Campaign Raises $600K for Muscular Dystrophy Association

News

Jiffy Lube raised more than $600,000 during its annual Muscle Up! drive, which continued its ongoing support of the Muscular Dystrophy Association (MDA) Summer Camp program, MDA Medical Care Centers, research efforts, and patient ... Read more

November 7, 2018November 7, 2018

Children’s National Health System Named PPMD Certified Duchenne Care Center

News

Expanding its network of institutions that provide standardized, comprehensive care for Duchenne patients, the Parent Project Muscular Dystrophy (PPMD) has named Children’s National Health System its newest Certified Duchenne Care Center ... Read more

November 5, 2018November 5, 2018

Pathway Key to Muscle Regeneration Doesn’t Work as It Should in Duchenne, Study Finds

News

The Hippo signaling pathway — a key regulator of tissue development, and cell growth and death — does not work as it should in Duchenne muscular dystrophy and acts to ... Read more

November 2, 2018November 2, 2018

Capricor’s Vesicle-based Therapy Holds Promise to Treat DMD, Preclinical Data Suggests

News

Capricor Therapeutics’ vesicle-based therapy CAP-2003, derived from the company’s proprietary cardiosphere-derived cells (CDCs), may be an effective therapy for Duchenne muscular dystrophy (DMD), according to preclinical data. The company ... Read more

October 31, 2018October 31, 2018

Cure Duchenne Kicks Off Inaugural ‘Pinkies Up to CureDuchenne’ Fundraising Campaign

News

A campaign hopes to raise awareness of Duchenne muscular dystrophy (DMD) and promote research toward a cure by asking supporters to paint a nail on one of their little fingers ... Read more

October 29, 2018

#NORDSummit – Major Issues on Table for Rare Disease Patients in US as Midterm Elections Approach

News

With the U.S. midterm elections now less than two weeks away, patient advocacy groups are solidly focused on a range of hot-button issues, from the Orphan Drug Tax Credit ... Read more

October 29, 2018October 29, 2018

Muscle Biopsy Aids Diagnosis, Treatment of Muscular Dystrophy in Children, Study Suggests

News

Muscle biopsies can benefit the diagnosis and treatment of neuromuscular diseases in children, particularly those with muscular dystrophy or inflammatory muscle disease, a study suggests. In the study, “Does muscle ... Read more

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