Clinical Trial Notification Program
Recent Posts
- What success looks like for me as a DMD parent
- FDA awards fast track designation to DM1 treatment DYNE-101
- Corticosteroid at low dose may help with muscle damage, inflammation
- Stuck in limbo with both accessible vans out of commission
- DYNE-101 is leading to functional gains for DM1 patients in trial
- How my FSHD progression leads to out-of-body experiences
- GIVI-MPC named FDA orphan drug for treatment of Becker MD
- My original diagnosis was incorrect. Here’s why that’s important.
- Waking up on Christmas Eve made me scared and anxious
- Gene-editing therapy for LGMD shows promise in mouse model