Clinical Trials

Recent Posts

• Being mindful of kidney stones while living with DMD
• FDA OKs trial to test gene therapy candidate in LGMD children
• Sarepta stops development of exon 51-skipping therapy for DMD
• Coping with grief and the day-to-day life of LGMD
• The missed milestones in the teenage years because of DMD
• Patients with certain mutations lose their walking ability earlier: Study
• I always try to pause to appreciate the small victories
• Supporting artists with disabilities through a new business venture
• Phase 1/2 trial of del-brax enrolling new, possibly pivotal FSHD group
• As a Duchenne mom, I know I can do hard things