Clinical Trials

Recent Posts

• Stuck in limbo with both accessible vans out of commission
• DYNE-101 is leading to functional gains for DM1 patients in trial
• How my FSHD progression leads to out-of-body experiences
• GIVI-MPC named FDA orphan drug for treatment of Becker MD
• My original diagnosis was incorrect. Here’s why that’s important.
• Waking up on Christmas Eve made me scared and anxious
• Gene-editing therapy for LGMD shows promise in mouse model
• How ‘The Remarkable Life of Ibelin’ moved me as a DMD survivor
• Application finalized for DMD cell therapy CAP-1002, now deramiocel
• My husband and I make a great team as we care for our sons