• Diagnosis​ ​Info​ ​and​ ​General​ ​Questions

  Potential Gene Therapy for Duchenne MD Could Improve Microdystrophin Production in Muscles

  Posted by MD forums Moderator on February 20, 2019 at 8:51 am

  Early findings in three Duchenne MD patients treated with SGT-001at low dose in a Phase 1/2 study show low levels of microdystrophin evident in muscles. Click here to learn more about what this could mean for patients with DMD.

  What are your thoughts on this news?

  MD forums Moderator replied 6 years, 1 month ago 1 Member · 0 Replies
• 0 Replies

Log In to Reply