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Recent Posts

• Changes this year helped me learn my limitations as a caregiver
• Regenxbio starts pivotal trial testing DMD gene therapy RGX-202
• How I experienced inclusion (and didn’t) during my education
• New technology may inform effective MD gene therapies: Study
• Being mindful of kidney stones while living with DMD
• FDA OKs trial to test gene therapy candidate in LGMD children
• Sarepta stops development of exon 51-skipping therapy for DMD
• Coping with grief and the day-to-day life of LGMD
• The missed milestones in the teenage years because of DMD
• Patients with certain mutations lose their walking ability earlier: Study