Duchenne muscular dystrophy (DMD) is caused by mutations in the dystrophin gene expressed in differentiated myofibers. Researchers at The Ottawa…
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BioBlast Pharma Ltd. has announced positive results from its Phase 2 open label clinical trial, HOPEMD, of Cabaletta (IV…
Lipid-lowering medications are used by many people to reduce risk of heart disease and other medical conditions. A new study…
Cellular models can elucidate molecular mechanisms underlying several diseases, reducing animal usage in biomedical sciences and following the guiding principles…
Researchers at the University of California published a study entitled “Human Satellite Cell Transplantation and Regeneration from…
A new study entitled “GRAF1 deficiency blunts sarcolemmal injury repair and exacerbates cardiac and skeletal muscle pathology…
A new report titled “Improving clinical trial design for Duchenne muscular dystrophy“, published in the journal…
New research out of Germany indicates that immune therapy might help treat Duchenne muscular dystrophy (DMD), a serious disease that…
Britain is now the first country in the world that allows the fusion of DNA from three people for the creation of…
PTC Therapeutics, Inc. submitted a New Drug Application (NDA) to the United States Food and Drug Administration (FDA) for Translarna™. The…