The effectiveness of Deflazacort (DFZ) against prednisone was tested in Duchenne muscular dystrophy (DMD) patients, and positive results were reported at the 2016…
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Researchers in Spain published a new report describing their search for myotonic dystrophy (DM1) biomarkers. Unfortunately, the search for miRNAs…
A recent article published in the Annals of Neurology describes promising results from a Phase 2b study of…
Muscular dystrophies (MDs) cause progressive weakness of muscles in young boys. Although treatments alleviate the symptoms and slow down disease…
Duchenne muscular dystrophy (DMD) is caused by mutations in the dystrophin gene expressed in differentiated myofibers. Researchers at The Ottawa…
BioBlast Pharma Ltd. has announced positive results from its Phase 2 open label clinical trial, HOPEMD, of Cabaletta (IV…
Lipid-lowering medications are used by many people to reduce risk of heart disease and other medical conditions. A new study…
Cellular models can elucidate molecular mechanisms underlying several diseases, reducing animal usage in biomedical sciences and following the guiding principles…
Researchers at the University of California published a study entitled “Human Satellite Cell Transplantation and Regeneration from…
A new study entitled “GRAF1 deficiency blunts sarcolemmal injury repair and exacerbates cardiac and skeletal muscle pathology…