An advisory committee of the European Medicines Agency (EMA) has issued another negative recommendation after re-examining a…
Articles by Alice Melão
A dysfunctional cerebellum leads to implicit learning deficits in children with Duchenne muscular dystrophy (DMD), Italian researchers have suggested.
Clinical data from a Phase 3 trial revealed that Kyndrisa (drisapersen) could not significantly improve the walking ability of…
Apple Tree Partners has invested $40 million in Stoke Therapeutics to come up with gene-expression treatments for muscular…
Treatment with Exondys 51 (eteplirsen) can prevent lung function decline in patients with Duchenne muscular dystrophy (DMD),…
UCLA researchers have developed a new method to efficiently produce and transplant functional skeletal muscle cells from human pluripotent stem…
Benitec Biopharma has submitted an application for orphan drug designation with the U.S. Food and Drug Administration (FDA) for…
The absence of a signaling protein leads to immature muscle cells being unable to fuse together to promote muscle tissue…
The researchers who developed the CRISPR DNA editing method that has taken medicine by storm have come up with a…
Infection by the influenza virus, commonly known as the flu, was found to contribute to muscle degeneration in a zebrafish model…