Long-term treatment with AOC 1001 continues to be safe and may reverse the progression of myotonic dystrophy type…
Articles by Andrea Lobo
SAT-3247, an oral therapy candidate for rebuilding muscle tissue, improved muscle function in a mouse model of facioscapulohumeral muscular…
Epic Bio’s epigenetic therapy EPI-321 has been granted an orphan drug designation by the U.S. Food and Drug Administration…
Fulcrum Therapeutics has completed patient enrollment for its Phase 3 clinical trial evaluating losmapimod as a potential treatment…
More than 420 “Fill the Boot” events will raise money throughout Labor Day weekend to advance research and care…
The U.S. Food and Drug Administration (FDA) has accepted and given priority review to Italfarmaco Group’s application requesting…
The U.S. Food and Drug Administration (FDA) has cleared Benitec Biopharma to start a Phase 1b/2a clinical trial of…
Stem cells derived from the amniotic membrane of pregnant women after childbirth “could provide therapeutic benefits” for people with…
Sarepta Therapeutics is calling for applications for the 6th annual Route 79, The Duchenne Scholarship Program, for the…
The European Commission (EC) has granted orphan drug designation to AB-1003, an investigational gene therapy for limb-girdle muscular dystrophy…