The French National Agency for Medicines and Health Products Safety has cleared Généthon to begin a clinical trial testing…
Articles by Forest Ray PhD
A new collaboration between Eli Lilly and Precision BioSciences aims to develop gene editing therapies for genetic disorders,…
Note: This story was updated Dec. 4, 2020, to note that Teji Singh’s title is executive medical director of Sarepta,…
The Myotonic Dystrophy Clinical Research Network (DMCRN) is asking adults with myotonic dystrophy type 1 (DM1) to participate…
The Muscular Dystrophy Association (MDA) and DNAnexus have introduced a digital platform to improve patient care and accelerate treatment…
The U.S. Food and Drug Administration (FDA) has given rare pediatric disease status to AMO Pharma‘s investigational therapy…
Italfarmaco has now completed recruitment — delayed in the spring due to the COVID-19 pandemic — of boys with…
September is Duchenne Action Month, an awareness, fund-raising, and educational campaign supporting people with Duchenne muscular dystrophy (DMD)…
Same But Different, a U.K. nonprofit that uses the arts to bring communities together, is holding a calendar photography…
NS Pharma‘s Viltepso (viltolarsen) is now commercially available in the U.S. for people with Duchenne muscular…