The U.S. Food and Drug Administration (FDA) and the European Commission (EC) have granted Orphan Drug designations…
Articles by Margarida Azevedo, MSc
The Muscular Dystrophy Association (MDA) and RYR-1 Foundation have announced an agreement to advance research and clinical care,…
The Muscular Dystrophy Association (MDA) will partner with the creative agency 50,000feet for the fifth year to help the nonprofit raise money…
The nonprofit Parent Project Muscular Dystrophy (PPMD) has awarded $239,000 to Dr. Terence Partridge, with the Research Center for Genetic Medicine at Children’s National Medical Center.
Catabasis Pharmaceuticals recently completed its target enrollment of 30 patients for the open-label extension of the Phase 2 portion (Part B)…
Elixirgen has announced the launch of its new Quick-Tissue 1.0 Series for use by scientists exploring new ways of…
Idera Pharmaceuticals recently presented preclinical data regarding the gene-silencing mechanisms of its third generation antisense (3GA) technology platform, a potential…
Capricor Therapeutics, Inc. announced that the U.S. Department of Defense (DoD) has awarded the company a $2.4 million grant to…
The U.S. Food and Drug Administration (FDA) has allowed an investigational new drug (IND) application for Carmeseal-MD in Duchenne…
The U.S. Food and Drug Administration (FDA) has granted Fast Track designation to Mallinckrodt’s investigational new drug (IND) application for…