Margarida Azevedo, MSc,  —

For the ninth year in a row, “Coach to Cure MD” and Parent Project Muscular Dystrophy (PPMD) will mark Duchenne Awareness Month  by using college football games to raise awareness of Duchenne muscular dystrophy (DMD) and money to promote research into treatments and a possible cure. The effort, a partnership between the…

The agency that plays the key role in European Union therapy authorizations has recommended against approval of Raxone (idebenone) as a Duchenne muscular dystrophy (DMD) treatment. Santhera said in a press release that it plans to appeal the Committee for Medicinal Products for Human Use’s decision, which covers Raxone in DMD patients not being treated…

PTC Therapeutics recently announced the recipients of the 2017 global Strategies to Realize Innovation, Vision and Empowerment (STRIVE) Awards program, recognizing excellence and innovation in the Duchenne muscular dystrophy (DMD) community. The 2017 awards were on World Duchenne Awareness Day, on Sept. 7. The STRIVE program was launched…

Parent Project Muscular Dystrophy is holding an awareness, fund-raising and educational campaign throughout September to fight Duchenne muscular dystrophy (DMD). It has scheduled events every day of Duchenne Action Month. You’ll find a calendar of activities here. September is traditionally a busy month for the worldwide DMD community.

The American Heart Association (AHA) has awarded its distinguished Scientist Development Grant to a University at Albany researcher for the development of new therapies to treat Duchenne muscular dystrophy (DMD). Bijan K. Dey, PhD, is a faculty researcher at the university’s RNA Institute and is working on a class of…

Continuing an 11-year tradition, the Muscular Dystrophy Association (MDA) will once again team up with Casey’s General Stores in Iowa to help send children with muscular dystrophy (MD) and related diseases away for a week of fun and friendship to MDA Summer Camp at no cost to their families. During…

The U.S. Food and Drug Administration (FDA) has granted Capricor Therapeutics rare pediatric disease designation for CAP-1002, its candidate therapy to treat  Duchenne muscular dystrophy (DMD). This latest approval, along with the FDA’s recent approval of orphan drug status to CAP-1002, “underscores the urgent need for treatment options for this devastating…

Parent Project Muscular Dystrophy (PPMD), a nonprofit working to end Duchenne muscular dystrophy (DMD), has recognized Gillette Children’s Specialty Healthcare Neuromuscular Clinic as a Certified Duchenne Care Center. The Certified Duchenne Care Center Program was launched by PPMD in March 2014 as part of its Transforming Duchenne Care Initiative.

We know dealing with muscular dystrophy sometimes feels like an uphill battle, both for the patients and the caregivers. You feel like you’re not doing enough or as if the disease is taking up all your time and attention. To help you on your journey, we’ve gathered a few quotes we…

Everest to End Duchenne, an organization raising funds to support research to end Duchenne muscular dystrophy, is looking for hikers, outdoor enthusiasts and climbers to take part in its second trek to Mount Everest Base Camp on Sept. 25. The treks represent the challenge that boys with Duchenne…