Parent Project Muscular Dystrophy (PPMD) is promoting a series of running events this year to raise money for research…
Articles by Margarida Azevedo, MSc
Researchers have received $119,999 in funding to test the effectiveness of a gene therapy approach in Charcot-Marie-Tooth neuropathy X type 1…
A Napa Valley fundraiser in Newport Beach, California, earlier this month attracted more than 400 people and raised at least…
Catabasis Pharmaceuticals will present results from Part B of the MoveDMD trial of edasalonexent (CAT-1004) for the treatment of Duchenne…
The Muscular Dystrophy Association (MDA) has awarded $7 million in grants to 29 top researchers for projects it says…
The U.S. Food and Drug Administration (FDA) acknowledged the filing over protest of PTC Therapeutics’ new drug application (NDA)…
Tens of thousands of businesses across the United States are taking part in this year’s 35th annual Muscular Dystrophy Association (MDA)…
ATyr Pharma’s Resolaris has received orphan drug status in the United States for the treatment of limb girdle muscular…
CureDuchenne Ventures will give Exonics Therapeutics $5 million to advance research on a gene editing technology known as CRISPR/Cas9 that…
Catabasis Pharmaceuticals reported mixed topline data from Part B of the MoveDMD trial evaluating the safety and efficacy of CAT-1004 (edasalonexent)…