Four months of treatment with the experimental oral therapy EDG-5506 reduced markers of muscle damage and improved measures of physical…
Articles by Marisa Wexler, MS
For the fourth year, a family in Montana is hosting “Calves to Cure,” a cattle auction that aims to…
Under an agreement with the Broad Institute, Sarepta Therapeutics has acquired an exclusive license to the gene therapy…
Sarepta Therapeutics plans to ask the U.S. Food and Drug Administration (FDA) to grant accelerated approval to the company’s…
The first participant has been dosed in the Phase 3 REACH clinical trial testing the safety and effectiveness of…
Pliant Therapeutics said it plans to ask the U.S. Food and Drug Administration (FDA) for permission to begin clinical testing…
The experimental oral therapy EDG-5506 has been generally well-tolerated and lowered markers of muscle damage among men with Becker…
The Muscular Dystrophy Association (MDA) is hosting a one-day games streaming fundraiser, dubbed “MDA Rivals,” this Saturday, June 18.
Reduced heart function is associated with a higher rate of mortality among people with Duchenne muscular dystrophy (DMD), a…
Treatment with glucocorticoids and heart medicines are key factors in determining the prognosis of Duchenne muscular dystrophy (DMD), according…