Despite broad initiatives seeking improvements, the time it takes an individual with Duchenne muscular dystrophy (DMD) to get a…
Articles by Marisa Wexler, MS
Treatment with the breast cancer medicine tamoxifen improved the functionality and survival of heart muscle cells in a cellular model…
The Spectrum Health Helen DeVos Children’s Hospital (HDVCH) in Michigan has been recognized as providing the highest quality of care…
An international team of scientists has developed a novel exon-skipping therapy mixture that has the potential to treat more than…
The U.S. Food and Drug Administration (FDA) has given Pfizer the go-ahead to open U.S. sites for the Phase…
A new natural history study that seeks to collect information about how Becker muscular dystrophy (BMD) progresses in the…
The European Commission is expected to propose a new governing framework for health data next month, called the European Health…
When it comes to making decisions about how care goals should change for adolescent and young adults with Duchenne…
Four boys with Duchenne muscular dystrophy (DMD) show improved motor function and walking ability three years after being given the…
Boys with Duchenne muscular dystrophy (DMD) treated with the experimental gene therapy SGT-001 in the IGNITE DMD clinical…