Posts by: Patricia Inacio, PhD

Capricor Therapeutics recently shared an update of the company’s quarterly financial results and operational highlights, including positive results for the ongoing HOPE study with Duchenne muscular dystrophy (DMD) patients. The Phase I/II HOPE study ... Read more

August 11, 2017August 11, 2017

Mitobridge’s Investigational DMD Therapy MA-0211 to Be Tested in Healthy Volunteers in Initial Clinical Trial

News

The investigational therapy MA-0211, also called MTB-1, a potential treatment for Duchenne Muscular Dystrophy (DMD), was approved for a Phase I clinical trial, developer Mitobridge announced. The trial will evaluate ... Read more

July 11, 2017

Most Common Congenital Muscular Dystrophy in UK Is MDC1A, 12-year Analysis Shows

News

A comprehensive 12-year genetic and clinical analysis of unrelated patients with congenital muscular dystrophies (CMDs) in the U.K. has confirmed MDC1A as the the most common CMD subtype, and ... Read more

July 10, 2017

Hand Braces During Sleep Can Help Preserve Muscle Function of Boys with Duchenne MD, Study Suggests

News

Overnight use of hand braces preserves hand function and delays the development of shortened muscles or joints in boys who have Duchenne muscular dystrophy (DMD), a study shows. The research, “Evaluation ... Read more

June 2, 2017June 2, 2017

MoveDMD Study Continuing to Progress, Catabasis CEO Says in Interview

News

MoveDMD (NCT02439216) is a three-part, ongoing clinical trial investigating an oral drug — edasalonexent (CAT-1004) — as a potential therapy in boys, ages 4 to 7, with Duchenne muscular dystrophy ... Read more

April 21, 2017April 21, 2017

Diagnosis of Muscular Dystrophies May Improve with RNA Sequencing, Study Shows

News

RNA sequencing may help to diagnose rare genetic muscle diseases — including muscular dystrophies — in people, according to the results of an international collaboration between several scientists. The study, ... Read more

March 9, 2017

Bone Health Varies Greatly Among FSHD Patients, Study Suggests

News

Bone health varies greatly among patients with facioscapulohumeral muscular dystrophy (FSHD), according to the results of a small group study, and tests for strength and functionality may identify those ... Read more

March 8, 2017

Heart Drug Inspra Improves Cardiac Function in Young Boys with DMD, Study Shows

News

Administration of Inspra (eplerenone) to young boys with Duchenne muscular dystrophy (DMD) improves their heart function and stabilizes it in older boys, a recent study shows. The study “Eplerenone ... Read more

March 6, 2017

Natural Sugar Fructose May Improve DMD Treatment Delivery, Mouse Study Suggests

News

The natural sugar fructose, commonly found in fruits and vegetables, may improve a type of treatment for Duchenne muscular dystrophy (DMD), according to researchers. The study, “Fructose Promotes Uptake and ... Read more

February 7, 2017

Strategies May Help Measure Muscle Function, Monitor Therapeutics in DMD Children

News

Two non-invasive strategies for measuring muscle function and its properties, electromechanical delay and ultrasound shear wave elastography, may help detect muscle impairments and assist in monitoring Duchenne muscular dystrophy ... Read more