Recent Posts
- Arrakis’ RNA-targeted oral therapies showing promise for DM1
- When art and advocacy meet onstage
- Sarepta to develop Arrowhead’s muscular dystrophy treatments
- Couch shopping awakened me to a focus on my children with DMD
- DMD carrier with heart failure has healthy pregnancy: Case study
- A walker should help prevent falls, right?
- DMD gene therapy GNT0004 set to enter Phase 3 trial in Europe, US
- Taking control when living with limb-girdle muscular dystrophy
- Changes this year helped me learn my limitations as a caregiver
- Regenxbio starts pivotal trial testing DMD gene therapy RGX-202