A look at Muscular Dystrophy subtypes and classification. Plus, global prevalence and incidence rates.
Videos: Rare Takes
In this video series, Muscular Dystrophy experts share their insights and best practices for diagnosing, managing, and treating DMD, including the importance of early diagnosis and collaborative decision-making.
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In this Guide
A look at Muscular Dystrophy subtypes and classification. Plus, global prevalence and incidence rates.
A comprehensive overview of the molecular mechanisms driving DMD and their relevance to disease progression and current therapeutic strategies.
Evidence-based management of DMD, including corticosteroids, disease-modifying therapies, cardiac and respiratory care, exon-skipping, and gene therapies.
From early recognition to characteristic physical findings and diagnostic evaluation, how to differentiate DMD from other muscular dystrophies.
How to approach CK screening, genetic testing, mutation classification, and muscle biopsy in DMD management.
From early motor symptoms to advanced cardiorespiratory disease, what to expect in DMD progression and prognostic factors.
Inside the emerging therapeutic landscape for DMD, including pharmacologic, gene, cell-based, and precision medicine approaches aimed at improving long-term clinical outcomes.