Posts by: Kara Elam

News

Monday’s announcement by the Food and Drug Administration (FDA) of accelerated approval for Exondys 51 (eteplirsen) injection, the first drug given approval for the treatment of Duchenne muscular dystrophy (DMD), ... Read more

July 22, 2016July 22, 2016

Integrin Protein May Lead to Potential Target for Muscular Dystrophy Therapies, Researchers Say

News

A protein known as integrin may play a key role in muscle tissue growth after injury or disease, a finding that could potentially lead to therapeutic targets for muscular ... Read more

March 30, 2016March 30, 2016

Sugar Molecule May Play Key Role in Muscular Dystrophy Treatment

News

Researchers at Japan’s Kobe University Graduate School of Medicine have successfully decoded a sugar molecule, providing an important step toward understanding a mechanism linked to muscular dystrophy (MD). The study, “Identification of ... Read more

March 23, 2016March 24, 2016

New Research Shows Strong Support for Muscular Dystrophy Screening in Newborns

News

Researchers from the University of Pittsburgh recently released key findings from a study which may hold important implications for novel therapies designed to treat patients with Duchenne muscular dystrophy ... Read more

January 14, 2016January 14, 2016

Idebenone Appears Promising as Treatment for Duchenne Muscular Dystrophy

News

A group of international researchers has published a review of clinical trials for a drug that shows significant potential as a therapy for people who suffer from Duchenne muscular ... Read more

December 8, 2015December 8, 2015

Duchenne MD Seen to Be Affected by Wnt Signaling Pathway

News

The Wnt signaling pathway might one day be a promising target for Duchenne muscular dystrophy (DMD) cognitive therapy, with potential clinical implications, according to a group of interdisciplinary researchers from universities throughout ... Read more

December 1, 2015December 2, 2015

Early Duchenne MD Study Finds Drug Strengthens Musculature

News

Researchers have treated a zebrafish animal model with a tyrosine kinase inhibitor to study its effect on fish musculature and strength in an experiment that shows promise for future therapeutic targets to ... Read more

November 3, 2015November 3, 2015

DMD Study Focus Is Pathophysiology of Dilated Cardiomyopathy

News

This week, a group of interdisciplinary researchers from universities throughout Italy released study findings with potentially important clinical implications for patients with Duchenne muscular dystrophy (DMD). The study, entitled ... Read more

July 1, 2015June 23, 2017

Catabasis Pharmaceuticals Begins MoveDMD Trial For The Treatment of Duchenne Muscular Dystrophy

News

Massachusetts based Catabasis Pharmaceuticals, a clinical-stage biopharmaceutical company focused on the discovery, development and commercialization of novel therapeutics based on their proprietary pathway pharmacology technology platform, recently announced that ... Read more

June 15, 2015June 15, 2015

Alzheimer’s Protein May Play Role In Eye Health And Muscle Strength Maintenance

News

This week researchers from the Institute for Neurodegenerative Disease, Massachusetts General Hospital (MGH), Harvard Medical School, released results from a study showing that a key protein associated with the ... Read more