The effects of glucocorticoid therapy and bisphosphonate treatment on tissue structure and bone matrix mineralization of nine boys with Duchenne…
Articles by Margarida Azevedo, MSc
Marathon Pharmaceuticals has announced the launch of ACCESS DMD, its expanded access program (EAP) to provide deflazacort to qualified patients with…
Results from a recent study published in the Journal of Pedriatric Orthopaedics showed full-time wheelchair use is…
Results from a study observing myotonic dystrophy type 2 (DM2) patients has helped pinpoint which disease symptoms are most important to…
Ringo, a golden retriever, has made an important contribution to science by helping researchers discover a gene that inhibits the consequences…
aTyr Pharma, Inc., has announced an expansion of its Phase 1b/2 clinical trial to continue the development and evaluation of efficacy…
ISIS Pharmaceuticals, a company focusing on the development of RNA-targeted drug discovery using its antisense technology platform, announced it earned a $2.8…
Ironwood Pharmaceuticals, Inc., recently announced the beginning of a Phase Ib clinical trial of IW-1973 and a Phase Ia clinical…
Recent research has demonstrated that early bisphosphonate treatment of a mice model of Duchenne muscular dystrophy (DMD) had some positive…
Professor Liza Pon, PhD, a leading researcher at the department of pathology and cell biology at Columbia University in New…