Clinical trial data suggest that edasalonexent — a potential Duchenne muscular dystrophy (DMD) therapy — does not affect the immune…
Articles by Marisa Wexler, MS
Final results of a Phase 1 clinical trial support the safety of losmapimod and suggest its effectiveness as a…
Sarepta Therapeutics has taken steps to ensure the supply of Vyondys 53 (golodirsen) and Exondys 51…
Machine learning could be used to help diagnose specific forms of muscular dystrophy (MD) using magnetic resonance imaging…
Capricor Therapeutics is expanding the development of exosome-based technologies that are being tested as a potential way to…
A new clinical trial is seeking about 80 people with limb-girdle muscular dystrophy type 2i (LGMD2i) to gather information…
Supplementing the diet with the amino acid L-arginine may improve gut function in people with Duchene Muscular Dystrophy…
Addressing changes in cellular metabolism and oxidative damage may lead to muscle regeneration in Duchenne muscular dystrophy and…
Translarna (ataluren) significantly improves physical fitness in people with Duchenne muscular dystrophy (DMD) and Becker muscular…
A new project called BIND — Brain Involvement iN Dystrophinopathies — seeks to better characterize how the brain is affected…