Both PTC Therapeutics and Sarepta Therapeutics expect to continue providing an uninterrupted supply of their Duchenne muscular dystrophy (DMD)…
Articles by Marisa Wexler, MS
The Muscular Dystrophy Association (MDA) has formed a Medical Advisory Team to provide guidance related to research and clinical…
Because of the global COVID-19 pandemic, Italfarmaco has paused enrollment of boys with Duchenne muscular dystrophy (DMD)…
The Muscular Dystrophy Association (MDA) is hosting an online Q&A session today to discuss the best ways that people…
Clinical trial data suggest that edasalonexent — a potential Duchenne muscular dystrophy (DMD) therapy — does not affect the immune…
Final results of a Phase 1 clinical trial support the safety of losmapimod and suggest its effectiveness as a…
Sarepta Therapeutics has taken steps to ensure the supply of Vyondys 53 (golodirsen) and Exondys 51…
Machine learning could be used to help diagnose specific forms of muscular dystrophy (MD) using magnetic resonance imaging…
Capricor Therapeutics is expanding the development of exosome-based technologies that are being tested as a potential way to…
A new clinical trial is seeking about 80 people with limb-girdle muscular dystrophy type 2i (LGMD2i) to gather information…