Enrollment Starts for Phase 2/3 Trial of Oral Therapy for Congenital DM1
AMO Pharma has begun enrollment for a Phase 2/3 trial that will assess the experimental oral therapy AMO-02 (tideglusib) in children and adolescents with congenital myotonic dystrophy type 1 (DM1). The randomized, double-blind trial (NCT03692312) is intended to support regulatory approval of AMO-02 for congenital…