News

Lipid-lowering medications are used by many people to reduce risk of heart disease and other medical conditions. A new study from Seattle, Washington, indicates an unexpected use of simvastatin, commonly known by the brand-name Zocor in the United States. According to the report, simvastatin may help skeletal muscles become more healthy in…

BioMarin Pharmaceutical, Inc. recently presented findings on Pompe disease along with two posters on Duchenne muscular dystrophy and Pompe disease during the ongoing 20th International Congress of the World Muscle Society in Brighton, England, which started September 30 and ran until October 4. The oral presentation on Pompe disease included preliminary…

Parent Project Muscular Dystrophy (PPMD), the largest and most comprehensive nonprofit organization in the US focused on finding a cure for Duchenne muscular dystrophy, recently announced it will collaborate with Sarepta Therapeutics, Inc, BioMarin Pharmaceutical Inc. and PTC Therapeutics for the upcoming phase of the very successful Decode Duchenne program.

In a recent study entitled “Human α7 Integrin Gene (ITGA7) Delivered by Adeno-Associated Virus Extends Survival of Severely Affected Dystrophin/Utrophin-Deficient Mice”, published in the Human Gene Therapy journal, a team of researchers from the Nationwide Children’s Hospital and the Ohio State University used gene therapy…

Cellular models can elucidate molecular mechanisms underlying several diseases, reducing animal usage in biomedical sciences and following the guiding principles for animal testing. Now, researchers at the Karolinska Institute and at the Karolinska University published a study entitled “Primary Murine Myotubes as a Model for Investigating Muscular…

Researchers at the University of California published a study entitled “Human Satellite Cell Transplantation and Regeneration from Diverse Skeletal Muscles” in the journal Stem Cell Reports whereby they reveal isolated human muscle stem cells capable of repairing damaged muscles. One of the major problems of treating…