30 Days of MD: Joe Logue
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30 Days of MD: Joe Logue
Muscular Dystrophy and Other Clinical Trials Adapting to Life With COVID-19
In a Facebook Live event hosted by the Muscular Dystrophy Association (MDA), experts discussed the effect that the COVID-19 pandemic has had on research efforts in muscular dystrophy, as well as the ongoing development of a potential COVID-19 vaccine. Clinical trials are a critical…
The Value of Having Friends With the Same Disease
Over the last couple of years, I’ve had opportunities to meet and befriend more adults with Duchenne muscular dystrophy. Whether we’ve found one another through CureDuchenne events or a common love for video games, my network within the…
September 19, 2020
by Kevin Schaefer
30 Days of MD: Jonathan “2J” Groenewald
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Real-world Data Could Replace Placebo Groups in DMD Clinical Trials, Study Indicates
Real-world and natural history data could be used to supplement, or perhaps replace, the use of a placebo in future clinical trials in people with Duchenne muscular dystrophy (DMD), a new study suggests. The study, “Suitability of external controls for drug evaluation in Duchenne muscular dystrophy,”…
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