30 Days of MD: Becky Bandy
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30 Days of MD: Becky Bandy
Sarepta Poised to Start Next Trial of SRP-9001 for Duchenne MD
Sarepta Therapeutics has completed a meeting with the Office of Tissues and Advanced Therapies (OTAT) that clarified regulatory requirements to start the company’s next clinical trial of SRP-9001, an investigational gene therapy for Duchenne muscular dystrophy (DMD). During the type C “written response only” meeting, the…
Overcoming the Idea of Being a Burden
As I’ve started relying more on people for things I used to do on my own, it’s become easier to ask for help without feeling like a burden. This toxic thought has been a challenging mental hurdle, but it’s one we all deserve to get over. With compassion,…
Differences in Key Proteins in DMD Muscle Cells Favor Fat Formation, Study Says
An imbalance in cells producing proteins called aldehyde dehydrogenases (ALDHs) — favoring fat formation in tissue — is evident in the muscles of people with Duchenne muscular dystrophy (DMD), a study reports. A better understanding of these cells could open new avenues of treatment, its researchers said. The…
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