Capricor Therapeutics will resubmit its application for U.S. Food and Drug Administration (FDA) approval of its cell therapy deramiocel to treat Duchenne muscular dystrophy (DMD)-related heart disease, following the agency’s decision to not accept the original filing. According to a company press release, the FDA issued a…
July is my favorite month. Many people who know me might be surprised by that, as they’re aware that I’m a Christmas enthusiast who loves to decorate, making my house look like the North Pole for nearly eight weeks every winter. I spend the other 10 months of the year…
Nearly one-third of people with muscular dystrophy (MD) experience moderate pain, which varies by the type of their MD, a study with more than 1,200 participants suggests. To manage their pain, about a fifth of patients used prescribed pain medications, mostly non-opioid therapies at first, then combined with opioids…
A couple weeks ago, I had the privilege of participating in a unique event designed for higher education students here in Singapore. It’s offered by Youth Corps Singapore to foster a sense of service among the next generation of leaders. As one of three ambassadors representing the Muscular Dystrophy…
Households incur substantial costs to accommodate people with Duchenne muscular dystrophy (DMD), according to a survey of patient caregivers in the U.S. Costs, such as those for purchasing and/or modifying an accessible vehicle, relocating to or building an accessible home, modifying home entrances, and buying medical equipment, were particularly…
The reward is that the chocolate cake tastes delicious and leaves you with a nice feeling. The risk is that you just spiked your sugar intake and may gain a few calories that take time and effort to burn off. The risk is that you may get injured, but the…
Summer vacation in the Midwest typically begins in mid-May, and kids return to school by mid-August. Here in Nebraska, that puts us halfway through summer break already. Like most moms, I’m feeling a mix of emotions: grief as I anticipate the end of these few precious weeks home with my…
Researchers identified a unique protein signature in the bloodstreams of adults with Becker muscular dystrophy (BMD) and limb-girdle muscular dystrophy (LGMD) that significantly differs from healthy individuals after exercise. “We propose that a subset of circulating proteins may be more indicative of disease progression and/or therapeutic efficacy than…
Summer is a great time to be outside, travel, attend neighborhood gatherings, and spend time with people you love. But those of us who live our adult lives with chronic illness face challenges in this season, as well as year-round. Still, there are many ways for us to enjoy…
Ifetroban, Cumberland Pharmaceuticals’ investigational oral therapy, improved heart function and reduced cardiac damage biomarkers in people with Duchenne muscular dystrophy (DMD), according to new trial data. These findings from the Phase 2 FIGHT DMD trial (NCT03340675) were presented at the Parent Project Muscular Dystrophy (PPMD) annual…
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