30 Days of MD: Melissa Soriano
30 Days of MD
View this post on Instagram Day 17 of 30 Days of MD Topic: School and MD This is @thesweetlifeofmel’s story: I never thought I’d go through a lot and ... Read more
Real-world Data Could Replace Placebo Groups in DMD Clinical Trials, Study Indicates
News
Real-world and natural history data could be used to supplement, or perhaps replace, the use of a placebo in future clinical trials in people with Duchenne muscular dystrophy (DMD), ... Read more
30 Days of MD: Becky Bandy
30 Days of MD
View this post on Instagram Day 16 of 30 Days of MD Topic: Love and MD This is Becky Bandy’s story: My name is Becky Bandy. I live in ... Read more
30 Days of MD: Leanne Watson
30 Days of MD
View this post on Instagram Day 15 of 30 Days of MD Topic: Changes and Challenges This is @leannes_wheel_life's story: The progressive physical effects of Adult Onset LGMD (Limb ... Read more
Sarepta Poised to Start Next Trial of SRP-9001 for Duchenne MD
News
Sarepta Therapeutics has completed a meeting with the Office of Tissues and Advanced Therapies (OTAT) that clarified regulatory requirements to start the company’s next clinical trial of SRP-9001, an ... Read more
30 Days of MD: Brad Miller
30 Days of MD
View this post on Instagram Day 14 of 30 Days of MD Topic: My Becker’s Story This is @mybeckersstory’s story: When I first started sharing my story through the ... Read more
Overcoming the Idea of Being a Burden
columns, Hawk's-Eye View - a Column by Hawken Miller
As I’ve started relying more on people for things I used to do on my own, it’s become easier to ask for help without feeling like a burden. This ... Read more
30 Days of MD: Clayton Theriault
30 Days of MD
View this post on Instagram Day 13 of 30 Days of MD Topic: Advocating for Disability Through My Blog and Video Podcast This is @cognizantclay’s story: Hello everyone! My ... Read more
30 Days of MD: Neil Kramer
30 Days of MD
View this post on Instagram Day 12 of 30 Days of MD Topic: Awareness and Advocacy This is @neil_kramer’s story: My name is Neil Kramer. The late Christopher Reeve ... Read more
30 Days of MD: Marie De Graaf
30 Days of MD
View this post on Instagram Day 11 of 30 Days of MD Topic: Accepting Life with Charcot-Marie-Tooth This [email protected]_charcotmarietooth ’s story: Shame. As a child I was ashamed of ... Read more
30 Days of MD: Crystal Rondeau
30 Days of MD
View this post on Instagram Day 10 of 30 Days of MD Topic: Medical Knowledge and MD This is @crystaleemarie’s story: I'm Crystal Rondeau and I have a form ... Read more
Differences in Key Proteins in DMD Muscle Cells Favor Fat Formation, Study Says
News
An imbalance in cells producing proteins called aldehyde dehydrogenases (ALDHs) — favoring fat formation in tissue — is evident in the muscles of people with Duchenne muscular dystrophy (DMD), ... Read more