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  • Firefighters to Hike 130 Miles to Raise Awareness of Neuromuscular Diseases and Promote Newborn Screening
  • Vamorolone Safely Aids Skeletal and Heart Muscle, Animal Study Finds
  • Brexit Could Have Real Effects for UK Rare Disease Patients, Experts Warn
  • Moral Dilemmas Complicate Treatment of Rare Diseases, Says Israeli Bioethicist
  • MDA’s 37th #MDAShamrocks Fundraiser is Underway
  • My First Time Attending the LA Abilities Expo
  • CureDuchenne Sets Calendar for Workshops, Sessions and ‘Futures’ Conference
  • MYO-101 Enables Production of Missing Protein in Children with LGMD2E, Trial Shows
  • Raxone (Idebenone) Shows Promise as DMD Therapy in SYROS Trial
  • NIH Rare Disease Day Highlights Joint Networks Advancing Array of Research
  • Join Us in the New Muscular Dystrophy News Forums