January 16, 2020January 15, 2020
Society Is Missing the True Definition of Inclusion
columns, Living, Learning, Thriving - a Column by Ralph Yaniz
My experiences writing this column over the past year have been fabulous. But it was daunting at first to ... Read more
January 15, 2020January 15, 2020
Montana Rancher’s ‘Calves to Cure DMD’ Funds Duchenne Research
News
Montana, the fourth-largest U.S. state in area, also is one of the least-populated — with maybe half a dozen ... Read more
January 14, 2020January 10, 2020
Regaining Control of My Life with The Happy Planner
columns, You, Me and MD - a Column by Leah Leilani
Most people with a chronic illness inevitably learn to expect the unexpected with their health. No matter how meticulously ... Read more
January 13, 2020January 13, 2020
Solid Biosciences Cuts Workforce, Restructures to Focus on SGT-001 Development
News
Solid Biosciences announced it will reduce its workforce by approximately one third to cut expenses and focus on advancing ... Read more
January 10, 2020January 10, 2020
Mount Everest Base Camp Trek Raises $60K for Duchenne Research
News
Tonya Dreher wanted to do something dramatic on behalf of Hope for Gus, the New Hampshire-based foundation inspired by her ... Read more
January 8, 2020January 8, 2020
PPMD Funds Gene Editing Research to Improve Cardiac Health, Muscle Function in Duchenne
News
Parent Project Muscular Dystrophy (PPMD) has granted $465,000 to Renzhi Han, PhD, a professor at the Ohio State University ... Read more
January 6, 2020January 2, 2020
Why Daily Stretching Is Important for Those with Duchenne Muscular Dystrophy
columns, Hawk's-Eye View - a Column by Hawken Miller
Stretching has been part of my daily life since I was diagnosed with Duchenne muscular dystrophy (DMD) about 17 ... Read more
January 6, 2020January 6, 2020
Astellas, Audentes Merger May Lead to New Exon-skipping Treatments for MD
News
Astellas Pharma recently agreed to acquire Audentes Therapeutics, a move it expects will result in faster development of potentially best-in-class ... Read more
January 3, 2020January 7, 2020
Top 10 Muscular Dystrophy Stories of 2019
News
Throughout 2019, Muscular Dystrophy News Today brought you daily coverage of important discoveries, treatment developments, clinical trials, and ... Read more
January 2, 2020January 2, 2020
Surviving Winter with Muscular Dystrophy
columns, Living, Learning, Thriving - a Column by Ralph Yaniz
I sometimes wonder how I will survive Chicago winters going forward. Winter is not a problem for some people ... Read more
December 20, 2019January 8, 2020
Vyondys 53 Available to Duchenne Patients in the U.S.
News
The newly approved therapy Vyondys 53 (golodirsen) is available for immediate distribution to treat people with Duchenne muscular dystrophy (DMD) amenable ... Read more
December 19, 2019December 19, 2019
New IGNITE DMD Trial Data Promising for SGT-001, Company Working to Lift Clinical Hold
News
Treatment with gene therapy candidate SGT-001 may lead to clinically meaningful improvements for patients with Duchenne muscular ... Read more

January 16, 2020January 15, 2020

Society Is Missing the True Definition of Inclusion

columns, Living, Learning, Thriving - a Column by Ralph Yaniz

My experiences writing this column over the past year have been fabulous. But it was daunting at first to put pen to paper to capture what so many people ... Read more

January 15, 2020January 15, 2020

Montana Rancher’s ‘Calves to Cure DMD’ Funds Duchenne Research

News

Montana, the fourth-largest U.S. state in area, also is one of the least-populated — with maybe half a dozen Duchenne muscular dystrophy patients among its 1.1 million inhabitants. One ... Read more

January 14, 2020January 10, 2020

Regaining Control of My Life with The Happy Planner

columns, You, Me and MD - a Column by Leah Leilani

Most people with a chronic illness inevitably learn to expect the unexpected with their health. No matter how meticulously I attempt to plan around my body’s needs, mitochondrial myopathy ... Read more

January 13, 2020January 13, 2020

Solid Biosciences Cuts Workforce, Restructures to Focus on SGT-001 Development

News

Solid Biosciences announced it will reduce its workforce by approximately one third to cut expenses and focus on advancing the development of SGT-001, its gene therapy candidate for the ... Read more

January 10, 2020January 10, 2020

Mount Everest Base Camp Trek Raises $60K for Duchenne Research

News

Tonya Dreher wanted to do something dramatic on behalf of Hope for Gus, the New Hampshire-based foundation inspired by her son, Gus, 14, who has Duchenne muscular dystrophy (DMD). In ... Read more

January 8, 2020January 8, 2020

PPMD Funds Gene Editing Research to Improve Cardiac Health, Muscle Function in Duchenne

News

Parent Project Muscular Dystrophy (PPMD) has granted $465,000 to Renzhi Han, PhD, a professor at the Ohio State University College of Medicine, to advance research into a targeted gene ... Read more

January 6, 2020January 2, 2020

Why Daily Stretching Is Important for Those with Duchenne Muscular Dystrophy

columns, Hawk's-Eye View - a Column by Hawken Miller

Stretching has been part of my daily life since I was diagnosed with Duchenne muscular dystrophy (DMD) about 17 years ago. Every night, my parents would reserve 30 minutes ... Read more

January 6, 2020January 6, 2020

Astellas, Audentes Merger May Lead to New Exon-skipping Treatments for MD

News

Astellas Pharma recently agreed to acquire Audentes Therapeutics, a move it expects will result in faster development of potentially best-in-class therapies for rare neuromuscular diseases, including muscular dystrophy (MD). Audentes’ ... Read more

January 3, 2020January 7, 2020

Surviving Winter with Muscular Dystrophy

columns, Living, Learning, Thriving - a Column by Ralph Yaniz

I sometimes wonder how I will survive Chicago winters going forward. Winter is not a problem for some people with neuromuscular disorders. But for those of us in colder ... Read more

December 20, 2019January 8, 2020

Vyondys 53 Available to Duchenne Patients in the U.S.

News

The newly approved therapy Vyondys 53 (golodirsen) is available for immediate distribution to treat people with Duchenne muscular dystrophy (DMD) amenable to exon 53 skipping, according to the medicine’s developer Sarepta Therapeutics. ... Read more

December 19, 2019December 19, 2019

New IGNITE DMD Trial Data Promising for SGT-001, Company Working to Lift Clinical Hold

News

Treatment with gene therapy candidate SGT-001 may lead to clinically meaningful improvements for patients with Duchenne muscular dystrophy (DMD), new data from two participants in the Phase 1/2 IGNITE ... Read more