Duvyzat (givinostat), a newly approved treatment for Duchenne muscular dystrophy (DMD), is now available in the U.S., according…
Articles by Marisa Wexler, MS
Most children with Duchenne muscular dystrophy (DMD) start experiencing notable issues with arm function and breathing ability before they…
The U.S. Food and Drug Administration (FDA) has given the green light for Myogenica to start a clinical trial…
Satellos Bioscience is gearing up to launch a Phase 1 clinical trial of its Duchenne muscular dystrophy (DMD)…
Treatment with the gene therapy BB-301 led to improved swallowing for the first person with oculopharyngeal muscular dystrophy…
With the first gene therapy for Duchenne muscular dystrophy (DMD) now approved in the U.S. for most people with…
Four experimental treatments — deramiocel, sevasemten, satralizumab, and tadalafil — all in clinical testing and all aiming to slow the…
In its 30-year history, Parent Project Muscular Dystrophy (PPMD) has helped fund the development of many experimental treatments for…
More than half a dozen exon-skipping therapies for Duchenne muscular dystrophy (DMD) — all seeking to increase production of…
Note: This story was updated Oct. 22, 2024, to remove a reference to the therapy being pulled from the…