The U.K. Adult North Star Network (ANSN) has developed a set of guidelines for best care management of adults with…
Articles by Marta Figueiredo, PhD
Upper limb strength, function, and muscle fat fraction continuously worsen over time in Duchenne muscular dystrophy (DMD) patients with…
A Phase 1 clinical trial evaluating Edgewise Therapeutics’ experimental oral therapy EDG-5506 in healthy volunteers and men with…
Brain abnormalities in people with adult-onset myotonic dystrophy type 1 (DM1) are significantly associated with cognitive impairment, apathy, and…
A team of researchers received a $3-million grant from the Chan Zuckerberg Initiative to create a comprehensive blueprint of…
The U.S. Social Security Administration (SSA) has added Duchenne muscular dystrophy (DMD) to its Compassionate Allowances (CAL) program…
A Phase 1b clinical trial evaluating Astellas Pharma’s ASP0367 is recruiting boys with Duchenne muscular dystrophy (DMD), ages 8–16, at…
Long-term treatment with Viltepso (viltolarsen) safely and effectively prevents a decline in motor function in boys with Duchenne…
CureDuchenne has launched the first comprehensive data hub to connect biosamples and clinical and genetic data from people with…
High levels of the toxic RNA molecule associated with myotonic dystrophy type 1 (DM1) lead to defects in muscle regeneration…