Posts by: Marta Figueiredo

News

Microdystrophin gene therapy robustly induces the production of a shorter, but functional, version of the dystrophin protein and reduces muscle damage in Duchenne muscular dystrophy (DMD) patients, according to ... Read more

February 12, 2018

New CRISPR Strategy Corrects Wider Range of Mutations Responsible for DMD

News

A new approach to CRISPR-Cas9 gene-editing technology, called myoediting, successfully restored dystrophin production and contraction force in heart muscle cells of Duchenne muscular dystrophy (DMD) patients. The new strategy, developed ... Read more

January 26, 2018

Ezutromid Reduces Muscle Damage in DMD Patients, Interim Data of Phase 2 Trial Shows

News

Ezutromid significantly reduced muscle damage in patients with Duchenne muscular dystrophy (DMD) after 24 weeks of treatment in a Phase 2 trial, Summit Therapeutics recently announced. DMD is a severe ... Read more

Posts by: Marta Figueiredo

Marta Figueiredo

Microdystrophin Gene Therapy Shows Promising Interim Results in Phase 1/2 Trial

New CRISPR Strategy Corrects Wider Range of Mutations Responsible for DMD

Ezutromid Reduces Muscle Damage in DMD Patients, Interim Data of Phase 2 Trial Shows

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