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Recent Posts

• How Duchenne Became My Unlikely Companion and Lifelong Partner in Crime
• Large1 Gene Helps MD Mice Live Longer by Restoring Muscle Function
• Rest Was Key for My COVID-19 Recovery With Duchenne MD
• Sometimes I’m Not Successful as a DMD Caregiver
• CRD’s Gene Editing Therapy Planned for DMD Patient After FDA Approval
• Sarepta Gains Rights to MyoAAV, Likely Vector for DMD Gene Therapy
• As My Sons Head Back to School, I’m Focusing on the Positives
• Rare Disease Groups Win Horizon’s #RAREis Global Advocate Grants
• Sarepta to Ask FDA to Approve DMD Gene Therapy SRP-9001
• Legos Remind Me of Our Family’s Legacy of Love