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Recent Posts
- EMA agency continues to oppose renewing Translarna’s approval
- Changing society and its views on disability, one column at a time
- I wish all of my sons could have played football
- RNA-based approach shows promise for DM1 in cell models
- An emergency preparedness plan is crucial for those with disabilities
- Gene therapy at low dose helps two OPMD patients with swallowing
- Every week, we try to organize chaos in our family of 9
- Capricor now seeking FDA approval of DMD therapy deramiocel
- C-Path to lead new task force seeking to advance LGMD therapies
- Educating all ages about living with muscular dystrophy